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Study Summary
No. 2007-0087:.......Leukemia; Lymphoma; Myeloma......Stefan Faderl......Leukemia
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Study Summary Title
Study Summary
Number:
2007-0087
Study Title:Multi-center, Open-label, Dose-escalating Phase I/II Trial of GS-9219 Administered Once Every Three Weeks Intravenously to Patients with Relapsed or Refractory Chronic Lymphocytic Leukemia or Non-Hodgkin's Lymphoma, or Multiple Myeloma
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Physician New Patient Referral
Name:Stefan FaderlPatients Call:800-392-1611 (in U.S.A.) 713-792-6161 (outside U.S.A.)
Dept:LeukemiaReferring MD
Call:
800-392-1611 (in U.S.A.) 713-792-6161 (outside U.S.A.)
Phone:713-745-4613
Contact us about clinical trials
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General Information
Disease Group:Leukemia
Lymphoma
Myeloma
Supported By:Gilead Sciences, Inc.
Phase of Study:Phase IReturn
Visit:
Patients should stay locally for the first cycle (21 days). Patients are asked
to return every 21 days for each cycle of therapy.
Treatment
Agents:
GS-9219Home Care:All treatment will be delivered at MDACC. Follow up evaluations (physical
examination, laboratory testing) can be done locally except for cycle 1.
Treatment Loc:Both at MDACC & outside MDACC at one or more Collaborating Sites or Institutions
Estimated
Length of Stay
in Houston:
About 24 hours of hospitalization during first infusion, the remainder of the
treatment is planned to be on an outpatient basis.
Description/
Intervention:
The goal of this clinical research study is to find the highest tolerable dose
of GS-9219 that can be given to patients with CLL, NHL, or MM. The safety and
effects of this drug will be studied. Researchers will also look at how the
body breaks down the drug.
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Study Objectives / Outcomes

Primary:

To assess the safety, toxicity, and maximum tolerated dose (MTD) of GS-9219 administered via IV administration once every three weeks (21 days) for six treatment cycles, i.e. for a total of 18 weeks, in patients with relapsed or refractory Chronic Lymphocytic Leukemia (CLL), Non-Hodgkin's Lymphoma (NHL), or Multiple Myeloma (MM).

Secondary:

To determine the pharmacokinetic parameters of GS-9219 for this regimen and patient population.

To assess the antitumor activity of GS-9219 based on Response Rate and Duration of Response. Progression-free Survival and Overall Survival will be assessed if applicable.

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Study Status Information
Study Activation / Registration Date:08/08/2007
IRB Review and Approval Date:05/15/2007
Study Type:Phase I
Recruitment Status:Terminated
Projected Accrual:62
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Enrollment Eligibility
If you do not meet the enrollment eligibility, there may be other treatment options for you. Please Contact the Referral Office for more information.

Inclusion Criteria:1) Age >/= 18 years

2) Subjects with relapsed or refractory CLL, NHL or MM. Patients are considered relapsed or refractory when showing evidence of disease progression after having either: at least two prior chemotherapy regimens, i.e., primary treatment and at least one salvage therapy. The therapies must include a single or multiple chemotherapy drugs with well documented activity in NHL, CLL, or MM to ensure that only patients with no know effective alternative therapy are included.

3) (Cont.) Antibodies such as rituximab, when given alone will not count as a primary or salvage therapy. Antibody therapy, given in combination with a single drug or a combination chemotherapy regimen will be considered one prior chemotherapy. Subjects with prior stem cell transplant (autologous or allogeneic) are eligible. Pre-induction chemotherapy with auto or allo transplant will be considered one prior chemotherapy, or a single high dose chemotherapy regimen that require bone marrow or stem cell support and in the opinion of the investigator no longer have potentially curable disease.

4) (continued) Subjects with CLL will be staged according to the Rai staging criteria. All patients in the Rai high-risk groups (i.e., Rai stages 3 and 4 based on the original five-stage system) are eligible. Intermediate risk patients (i.e., Rai stages 1 and 2 based on the original five-stage system) with one or more signs of active disease (such as progressive lymphocytosis, lymphadenopathy, splenomegaly, weight loss > 10% within six months, extreme fatigue, fever and/or night sweats without evidence of infection) are also eligible.

5) (continued) Subjects with NHL will be staged according to the Ann Arbor classification and must present with bi-dimensionally measurable disease either on physical examination or on imaging studies. Any tumor mass measurable in two dimensions and >/= 2 cm in its longest transverse diameter is acceptable (or >/= 1.5 cm in its longest transverse diameter if 0.5 cm slices are used as in spiral CT scans).

6) Eastern Cooperative Oncology Group (ECOG) Performance Status of 0, 1, or 2.

7) Subjects must demonstrate adequate organ function during the Screening Period and at the Cycle 1 Pre-Dose assessment as defined below: Dose Escalation (Part A Only): Hematology: Absolute neutrophil count (ANC) >/= 1,500 cells/mm3, Platelets >/= 100,000/mm3, and Hemoglobin >/= 8.5 g/dL; Liver Function: Total serum bilirubin within normal range, Aspartate transaminase (AST) </= 3 times ULN, and Alanine transaminase (ALT) </= 3 times ULN; Renal Function: Serum creatinine </= 1.5 mg/dL

8) Electrocardiogram (ECG) without evidence of clinically significant ventricular arrhythmias, conduction abnormalities, or active ischemia as determined by the Investigator. Pulmonary function test, chest x-ray or CT scan of the chest if not performed within 4 weeks before dosing of study drug (GS-9219). The pulmonary function testing and chest x-ray are done to record lung conditions before study dosing, in case respiratory symptoms are developed during the study.

9) Males and females of childbearing potential (less than 1 year postmenopausal or no history of hysterectomy, bilateral tubal ligation, or bilateral oophorectomy) must agree to utilize a highly effective method of contraception throughout the study period and for 30 days following discontinuation of study drug. A highly effective method of birth control is defined as a method that results in a low failure rate (i.e., less than 1% per year) when used consistently and correctly, such as implants, injectables, combined oral contraceptives, some IUDs, sexual abstinence, or a vasectomized partner.

10) Ability to understand and willingness to sign a written informed consent document.

11) Subjects with MM will be staged according to the International Staging System (ISS) (Appendix 10 of protocol). All patients with Stage II or III disease are eligible. Subjects must have secretory and measurable disease [measurable defined as one or more of the following: serum M-protein >/= 1 g/dL by serum protein electrophoresis, urine M-protein >/= to 200 mg/24 hours, serum free light chain (FLC) measurement >/= 10 mg/dL provided serum FLC ratio is abnormal.]

12) MTD Expanded Cohort (Part B Only): Hematology - Absolute neutrophil count (ANC) - 1,000 cells/mm3; Platelets - 50,000/mm3, and Hemoglobin - 8.0 g/dL; Liver Function - total serum bilirubin within normal range; Aspartate transaminase (AST) - 2.5 times ULN; Alanine transaminase (ALT) - 2.5 times ULN; Renal function - serum creatinine 3.0 mg/dL.

Exclusion Criteria:1) Subjects with AIDS-related lymphoma.

2) Subjects with NHL who present exclusively with non-measurable lesions. Lesions that are considered intrinsically non-measurable include the following: bone lesions; leptomeningeal disease; ascites; pleural/pericardial effusion; inflammatory breast disease; lymphangitis cutis/pulmonis; abdominal masses that are not confirmed by imaging techniques; cystic lesions; and lesions that are situated in a previously irradiated area.

3) Recent anticancer therapy: Dose Escalation (Part A Only). Patients who underwent chemotherapy, radiotherapy, and/or biotherapy within four weeks (at least 12 weeks for stem cell transplantation) prior to starting treatment with GS 9219 are excluded. MTD Expanded Cohort (Part B Only): Patients who previously underwent chemotherapy, radiotherapy, any major surgery, and/or biotherapy must have recovered from reversible toxicities to CTCAE Grade 1 or less, except as otherwise described in Inclusion Criteria for Part B.

4) Use of any investigational agents within four weeks prior to starting treatment with GS 9219.

5) Other concurrent malignancy. Patients with a history of basal or squamous cell skin cancer and/or in situ cervical cancer who were treated adequately and with curative intent may be enrolled. Patients with a history of any other cancer who have been disease-free for at least two years may be enrolled if carefully assessed at the time of study entry to rule out recurrence of the other cancer.

6) Women who are pregnant or breast feeding.

7) Uncontrolled concurrent illness including, but not limited to, human immunodeficiency virus (HIV)-positive subjects receiving antiretroviral therapy, hepatitis of any etiology, ongoing or active infection requiring systemic antibiotic, New York Heart Association class III or IV heart disease, unstable angina pectoris, ventricular arrhythmia, or psychiatric illness/social situations that would limit compliance with study requirements.

8) Patients on chronic, systemically administered steroids. Dose Escalation (Part A Only): Patients on chronic systemically administered steroids, with the exception of inhaled steroids, MTD Expanded Cohort (Part B Only): Patients on chronic, stable dose of systemically administered steroids for a non-malignant condition must have clear evidence of progressive disease to rule out an anti-cancer effect of the steroids.

9) Known hypersensitivity to nucleoside analogues in general, the study drug, the metabolites or formulation excipients.

10) Subjects with MM who have non-secretory and/or non-measurable disease.

11) Subjects with evidence of pulmonary fibrosis on chest X-rays.

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Links
Registration Number: NCT00499239
Study Information on Clinical Trials Registry (clinicaltrials.gov)

Other Links:
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Results


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