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Study Summary
No. 2007-0102:.......Infection......Issam Raad......Infection Control/Infectious Diseases & Employee Health
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Study Summary Title
Study Summary
Number:
2007-0102
Study Title:A phase III, Double blind, randomized study to evaluate safety and efficacy of Isavuconazole (BAL 8557) versus Voriconazole for primary treatment of invasive fungal disease caused by aspergillus species or other filamentous fungi.
( Sponsor number # WSA-CS-004)
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Physician New Patient Referral
Name:Issam RaadPatients Call:800-392-1611 (in U.S.A.) 713-792-6161 (outside U.S.A.)
Dept:Infection Control/Infectious Diseases & Employee HealthReferring MD
Call:
800-392-1611 (in U.S.A.) 713-792-6161 (outside U.S.A.)
Phone:713-792-7943
Contact us about clinical trials
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General Information
Disease Group:InfectionSupported By:Astellas Pharma Global Development Inc.
Phase of Study:Phase IIIReturn
Visit:
Minimum 3 return visits will be arranged for patient respectively at Day 42,
Day 84/EOT, and 4 weeks after EOT and/or as clinically indicated.
Treatment
Agents:
Isavuconazole (BAL8557)
Voriconazole
Home Care:Once switched to oral medication, the patient can be released from the hospital
while remaining in the study and will be treated by the PI as clinically
indicated.
Treatment Loc:Both at MDACC & outside MDACC at one or more Collaborating Sites or Institutions
Estimated
Length of Stay
in Houston:
Minimum 3 days in hospital as soon as patient can be switched from IV to oral
therapy as clinically indicated.
Description/
Intervention:
The goal of this clinical research study is to compare Isavuconazole (ISA) with
Voriconazole (VRC) to find out which treatment may better help control an
invasive fungal infection, such as aspergillus or other molds. The safety of
isavuconazole will also be studied.
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Study Objectives / Outcomes
Primary Objective:
  • To compare all-cause mortality through Day 42 following primary treatment with
isavuconazole versus voriconazole (VRC) in patients with IFD caused by Aspergillus species or other filamentous fungi.

Secondary Objectives:
  • To compare the effects of treatment on:
      - All-cause mortality rate at Day 84
      - Overall outcome at Day 42, End of Treatment (EOT) and Day 84
      - Overall outcome at Day 42, EOT and Day 84 in patients with mycologically confirmed
      lower respiratory tract disease (LRTD)
      - Overall outcome and mycological response at Day 42, EOT and Day 84 in the
      subpopulations defined by the stratification variable
      - Mycological response at Day 42, EOT and Day 84
  • To characterize the safety and tolerance of treatment with ISA

Exploratory Objectives:
  • To characterize the pharmacokinetics (PK) of study drug and metabolite(s) if warranted in the PK subpopulation
  • To characterize pharmacokinetic (PK) trough values of study drug and metabolite(s) if warranted
  • To evaluate the use of serum galactomannan as a biomarker for overall response in patients with invasive aspergillosis.
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Study Status Information
Study Activation / Registration Date:07/13/2007
IRB Review and Approval Date:05/11/2007
Study Type:Phase Iii
Recruitment Status:Open
Projected Accrual:510
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Enrollment Eligibility
If you do not meet the enrollment eligibility, there may be other treatment options for you. Please Contact the Referral Office for more information.

Inclusion Criteria:1) Patients and/or legally authorized representative(s), if applicable, who have been fully informed and have given voluntary written informed consent or patients unable to write and/or read but who fully understand the oral information given by the Investigator (or nominated representative) who have given oral informed consent witnessed in writing by an independent person.

2) Ability and willingness to comply with the protocol.

3) Male and female patients aged equal to and/or greater than 18 years.

4) Female patients must be non-lactating and at no risk for pregnancy for one of the following reasons: 1) Postmenopausal for at least 1 year; 2) Post-hysterectomy and/or post-bilateral ovariectomy; 3) If of childbearing potential, having a negative urine or serum human chorionic gonadotropin (hCG) pregnancy test at the screening visit and be using a highly effective method of birth control throughout the course of the study. Reliable sexual abstinence throughout the course of the study is acceptable as a highly effective method of birth control for the purposes of this study.

5) Patients with proven IFD caused by Aspergillus species or other filamentous fungi as defined below. 1) Patients with a positive diagnostic test (histology/ cytology or galactomannan (GM) antigen) obtained prior to the first dose and up to 7 days after the first administration of study medication 2) Patients with mold from a sample for culture obtained by a sterile procedure from a normally sterile and clinically or radiologically abnormal site consistent with an infectious disease process, e.g. transbronchial biopsy, open-lung biopsy, or brain biopsy. 3) Patients with a blood culture that yields a mold (e.g. Fusarium species) in the context of a compatible infectious disease process except for in an immunocompetent host where a blood culture that yields Aspergillus species is to be considered a contaminant and the patient is not eligible for enrollment.

6) Patients with probable or possible IFD caused by Aspergillus species or other filamentous fungi as defined below: Probable IFD: At least one host factor [a] PLUS At least one clinical feature [b] PLUS At least one mycological criterion [c] as defined in sponsor protocol. Possible IFD: At least one host factor [a] PLUS At least one clinical feature [b] . Note that Patients fulfilling the criteria for possible IFD as defined above will be eligible for enrollment; however, furthur confirmatory results as detailed in sponsor protocol will be required within 7 days after the first administration of study medication.

Exclusion Criteria:1) Women who are pregnant or breastfeeding.

2) Known history of allergy, hypersensitivity to or any serious reaction to the azole class of antifungals or to any component of the study medication.

3) Patients for whom VRC is contra-indicated, including cardiovascular findings.

4) Patients at high risk for QT/QTc prolongation such as: 1) Baseline prolongation of QTcF ³ 500 msec. 2) Risk factors for Torsade de Pointes (e.g. uncompensated heart failure, abnormal potassium or magnesium levels that cannot be corrected, any unstable cardiac condition during the last 30 days, or a family history of long QT syndrome). 3) The use of concomitant medications that prolong the QT/QTc interval.

5) Evidence of moderate to severe hepatic or renal dysfunction with any of the following abnormal laboratory parameters at the screening visit: (1) Total bilirubin is equal to or more than 3 times the upper limit of normal (ULN); (2) Alanine transaminase (ALT) or aspartate transaminase (AST) is equal to or more than 5 times ULN; (3) Patients with known cirrhosis or chronic hepatic failure. 4) Calculated creatinine clearance (CLcr) < 50 mL/minute at screening 5) Patients on dialysis or likely to require dialysis while on medication.

6) Concomitant use of sirolimus, efavirenz, ritonavir, astemizole, cisapride, rifampicin, rifabutin, ergot alkaloids, long acting barbiturates, carbamazepine, pimozide, quinidine, neostigmine, ketoconazole, valproic acid, St. John's Wort or terfenadine, in the 5 days prior to first administration of study drug .

7) Patients with any other invasive fungal infection other than Aspergillus species or other filamentous fungi and patients with Zygomycetes or Scedosporium prolificans infection not expected to respond to voriconazole treatment.

8) Patients with either chronic aspergillosis, aspergilloma, or ABPA.

9) Microbiological (e.g. virological) findings or other potential conditions that are temporally related and suggest a different etiology of the clinical features.

10) Patients who have been administered more than 4 cumulative days of itraconazole, voriconazole, or posaconazole, for any reason, within the 7 days prior to the first administration of study medication.

11) Advanced human immunodeficiency virus infection with CD4 count is less than 200 or acquired immunodeficiency syndrome-defining condition, body weight is less than 40 kg.

12) Any known or suspected condition of the patient that may jeopardize adherence to the protocol requirements or impede the accurate measurement of efficacy (e.g. neutropenia not expected to resolve, patients with endocarditis, osteomyelitis, meningitis, tracheobronchitis, or uncontrolled malignancy with life expectancy of less than 30 days).

13) Patients with a concomitant medical condition that, in the opinion of the investigator, may be an unacceptable additional risk to the patient should he/she participate in the study.

14) Patients previously enrolled in this study.

15) Treatment with any investigational drug in any clinical trial within 30 days prior to the first administration of study medication except unblinded phase III trials.

16) Patients who are unlikely to survive longer than 30 days or patients on mechanical ventilation.

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Links
Registration Number: NCT00412893
Study Information on Clinical Trials Registry (clinicaltrials.gov)

Other Links:
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Results


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