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Study Summary
No. 2007-0421:.......Advanced Cancers; Bone; Brain; CNS; Genitourinary; Kidney; Liver; Ovary; Pediatrics; Phase I Studies; Sarcoma; Solid Tumors; Testis......Cynthia E. Herzog......Pediatrics
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Study Summary Title
Study Summary
Number:
2007-0421
Study Title:Multiple Ascending Dose (MAD) Phase I Study of the
IGF-1R Antagonist R1507 Administered as an Intravenous Infusion in
Children and Adolescents with Advanced Solid Tumors
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Physician New Patient Referral
Name:Cynthia E. HerzogPatients Call:800-392-1611 (in U.S.A.) 713-792-6161 (outside U.S.A.)
Dept:PediatricsReferring MD
Call:
800-392-1611 (in U.S.A.) 713-792-6161 (outside U.S.A.)
Phone:713-792-6620
Contact us about clinical trials
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General Information
Disease Group:Advanced Cancers
Bone
Brain
CNS
Genitourinary
Kidney
Liver
Ovary
Pediatrics
Phase I Studies
Sarcoma
Solid Tumors
Testis
Supported By:F. Hoffmann-La Roche LTD
Phase of Study:Phase IReturn
Visit:
Drug infusions: Either once weekly on Day 1 or 3 times weekly on Days 1, 8,
and 15. PKs: On Days 1, 2, 3 and 4 or 1st cycle. Follow-up off-study: Days 7
and 30.
Treatment
Agents:
R1507Home Care:None.
Treatment Loc:Both at MDACC & outside MDACC at one or more Collaborating Sites or Institutions
Estimated
Length of Stay
in Houston:
No hospitalization required.
Description/
Intervention:
The goal of this clinical research study is to learn the pharmacokinetics (PK)
and pharmacodynamics (PD) of R1507. PK testing measures the amount of study
drug in the body at different time points. PD testing measures the amount of
tumor markers in the blood at different time points. The safety and
tolerability of the study drug will also be studied.
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Study Objectives / Outcomes
Primary Objectives

• To determine the doses of R1507, a monoclonal antibody to the Type I Insulin-like Growth Factor Receptor (IGF-1R), that achieve serum drug exposure levels (AUCs) in children and adolescents with advanced solid tumors that are equivalent to the exposures in adults at the adult recommended doses of 9 mg/kg administered on a weekly schedule and 16 mg/kg administered every 3 weeks.
• To determine the maximum tolerated doses of R1507 in children and adolescents with advanced solid tumors IF dose-limiting toxicity is observed in 2 or more patients at any dose level on the weekly or every 3 week schedules.

Secondary Objectives

• To determine the maximum tolerated doses of R1507 in children and adolescents with advanced solid tumors IF dose-limiting toxicity is observed in 2 or more patients at any dose level on the weekly or every 3 week schedules.
• To describe the pharmacokinetic profile of R1507 after single and repeated dosing in children and adolescents with advanced solid tumors.
• To describe any anti-tumor responses to R1507.
• To describe the early effects of R1507 on tumors by PET scan.
• To investigate the expression of IGF-related signaling pathways in archival tumor tissue using immunohistochemistry.
• To assess the development of an immunologic response (HAHA) to R1507.
• To assess changes in IGF-1R related signaling molecules in patient serum samples
• To determine the appropriate dose of R1507 for further diseasedirected/phase II studies in children and adolescents with advanced solid tumors.
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Study Status Information
Study Activation / Registration Date:11/13/2007
IRB Review and Approval Date:08/30/2007
Study Type:Phase I
Recruitment Status:Terminated
Projected Accrual:58
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Enrollment Eligibility
If you do not meet the enrollment eligibility, there may be other treatment options for you. Please Contact the Referral Office for more information.

Inclusion Criteria:1) AGE: >/= 2 years to < 18 years of age.

2) DIAGNOSES: Histologically confirmed solid tumors, which may include but are not limited to rhabdomyosarcoma and other soft tissue sarcomas, Ewing sarcoma family of tumors, osteosarcoma, neuroblastoma, Wilms' tumor, hepatic tumors, germ cell tumors, and primary brain tumors. In patients with brain stem or optic gliomas the requirement for histological confirmation can be waived if a biopsy was not performed.

3) TUMOR STATUS: Measurable or evaluable tumors. Patients with neuroblastoma that is only detectable by MIBG are eligible and considered to have measurable disease using the Curie scale. Patients with neuroblastoma that is only detected by bone marrow aspirate/biopsy are eligible and considered to have evaluable disease.

4) PRIOR THERAPY: The patient's cancer must have relapsed after or failed to respond to frontline curative therapy or there must not be other potentially curative treatment options available. Curative therapy may include surgery, radiation therapy, chemotherapy, or any combination of these modalities. Patients must have fully recovered to grade </=1 from the acute toxic effects of all prior chemotherapy, immunotherapy, or radiotherapy prior to entering this study.

5) Myelosuppressive chemotherapy: The last dose of all myelosuppressive anticancer drugs must be at least 3 weeks prior to study entry.

6) Biologic (anti-cancer agent): The last dose of all biologic agents for the treatment of the patient's cancer (such as retinoids) must be at least 7 days prior to study entry. The last dose of other monoclonal antibodies must be at least 30 days prior to study entry.

7) Investigational anti-cancer agent: The last dose of all investigational agents must be at least 30 days prior to study entry.

8) Radiation therapy: The last dose of radiation (including therapeutic ^131 MIBG) to more than 25% of marrow containing bones (pelvis, spine, skull) must be at least 4 weeks prior to study entry. The last dose of all other local palliative (limited port) radiation must be at least 2 weeks prior to study entry.

9) Stem Cell Transplantation. Patients must be at least 2 months post-autologous transplant and must have recovered from toxicities. Patients must be at least 6 months post-allogeneic transplant, must have recovered from toxicities, and must have no evidence of active graft-versus-host disease. Patients must also have been off of immunosuppressive treatment at least 30 days.

10) Number of prior treatment regimens: No limitation on the number of prior chemotherapy regimens that the patient may have received prior to study entry.

11) Colony stimulating factors: The last dose of colony stimulating factors, such as filgrastim, sargramostim, and epoetin, must be at least 48 hours prior to study entry, and the last dose of long-acting colony stimulating factors, such as pegfilgrastim, must be at least 10 days prior to study entry.

12) PERFORMANCE SCORE: 60-100 (Karnofsky scale, for patients >/=10 years of age) or 60-100 (Lansky scale, for children younger than 10 years of age).

13) HEMATOLOGIC FUNCTION: (a) Absolute neutrophil count (ANC) >/= 1.5 x 10^9/L; (b) Platelet count >/= 100 x 10\^9/L; (c) Patients with an ANC < 1.5 x 10^9/L or platelet count < 100 x 10^9/L due to bone marrow involvement by tumor or the effects of prior therapy are eligible only for the expanded cohort at the optimal dose/MTD on the qW schedule, but will not be evaluable for hematological toxicity. These patients should have an ANC > 0.5 x 10^9/L and a platelet count > 50 x 10^9/L.

14) RENAL FUNCTION: Age-adjusted normal serum creatinine OR a creatinine clearance >/= 60 mL/min/1.73 m^2 based on a 24 h urine collection. Normal Serum Creatinine in Children (maximum): 2 yrs to < 6 yrs: 0.8 mg/dl; 6 yrs to < 10 yrs: 1 mg/dl; 10 yrs to < 13 yrs: 1.2 mg/dl; 13 yrs to < 16 yrs: Male, 1.5 mg/dl, Female, 1.4 mg/dl; > 16 yrs: Male, 1.7 mg/dl, Female, 1.4 mg/dl.

15) HEPATIC FUNCTION: (a) Serum total bilirubin < 1.5 x ULN; (b) ALT/AST </= 2.5 x the ULN (</= 5 x the ULN for patients with known hepatic metastases).

16) CARDIAC FUNCTION: Left Ventricle Shortening fraction >/=28% (or equivalent left ventricular ejection fraction > 45%) by echocardiogram.

17) Patients with CNS metastases are eligible for enrollment if they have received prior surgical resection of or radiotherapy to site(s) of CNS disease and have been off corticosteroids for at least 4 weeks. Neurological deficits in these patients must have been stable for at least 4 weeks.

18) Patients enrolled on the dose escalation portion of the trial must being willing to participate in the pharmacokinetic studies that are performed on cycle 1, because this represents the primary endpoint of the trial. Pharmacokinetic studies are optional in patients enrolled in the expanded cohort at the optimal dose/MTD.

19) Patients and their legal representatives must be able to read, understand and provide written informed consent to participate in the trial.

20) Females of childbearing potential as well as fertile males and their partners must agree to use an effective form of contraception during the study and for 120 days following the last dose of study medication (effective forms of contraception include abstinence, a contraceptive or a double barrier method).

Exclusion Criteria:1) Active infection or fever >/= 38.5 degrees Celsius within 3 days of the first scheduled day of dosing unless the fever is felt to be tumor-related.

2) Treatment with pharmacologic doses of corticosteroids within the past 4 weeks; current or past use of anti-IGF-1R antibodies; current treatment with immunosuppressive agents.

3) Known hypersensitivity to any of the components of R1507 or who have had prior hypersensitivity reactions to monoclonal antibodies.

4) Patients who are receiving concurrent investigational therapy (agents that have no FDA approved indication) or who have received investigational therapy within a period of 30 days prior to the first scheduled day of dosing. Investigational therapy is defined as treatment for which there is currently no FDA approved indication.

5) Patients with diabetes mellitus defined as: (a) Casual serum glucose concentration of >/= 200 mg/dL; (b) Fasting serum glucose of >/= 125 mg/dL; (c) Need for use of an oral hypoglycemic agent or insulin in order to keep the serum glucose below the above levels.

6) Severe uncontrolled systemic disease.

7) Patients who are pregnant or breast feeding.

8) Patients with reproductive potential not willing to use an effective method of contraception, which includes abstinence.

9) Any other medical condition, including mental illness or substance abuse, deemed by the Investigator to be likely to interfere with a patient's ability to sign informed consent, cooperate and participate in the study, or interfere with the interpretation of the results.

10) Known HIV or Hepatitis B or C (active, previously treated or both).

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Links
Registration Number: NCT00560144
Study Information on Clinical Trials Registry (clinicaltrials.gov)

Other Links:
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Results


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