Return to List

Study Summary
No. 2008-0693:.......Sarcoma......Vinod Ravi......Sarcoma Medical Oncology
.
Study Summary Title
Study Summary
Number:
2008-0693
Study Title:A randomized, open-label, multi-center phase III study to evaluate the efficacy and safety of nilotinib versus imatinib in adult patients with unresectable or metastatic gastrointestinal stromal tumors (GIST)
.
Physician New Patient Referral
Name:Vinod RaviPatients Call:800-392-1611 (in U.S.A.) 713-792-6161 (outside U.S.A.)
Dept:Sarcoma Medical OncologyReferring MD
Call:
800-392-1611 (in U.S.A.) 713-792-6161 (outside U.S.A.)
Phone:713-792-3626
Contact us about clinical trials
.
General Information
Disease Group:SarcomaSupported By:Novartis
Phase of Study:Phase IIIReturn
Visit:
Main protocol-Pre-study visit. Day 1, day 8, day 28, then every 3 months.
Extension Study-visits will be every 3 months.
Treatment
Agents:
Imatinib
Nilotinib
Home Care:Patients will be randomized to receive either Nilotinib or Imatinib. Patients
will self administer Nilotinib or Imatinib at home.
Treatment Loc:Both at MDACC & outside MDACC at one or more Collaborating Sites or Institutions
Estimated
Length of Stay
in Houston:
N/A
Description/
Intervention:
The goal of the extension part of this study is to learn if patients with GIST,
who no longer respond to imatinib or nilotinib therapy that is given as part of
this study, would benefit from taking the other study drug they did not take.

In addition, the extension study now offers patients who received nilotinib in
the core study the possibility to be treated with imatinib prior to disease
progression.
.
Study Objectives / Outcomes
Primary objectives
  • To compare progression free survival (PFS) of nilotinib and imatinib when used as initial therapy in the above specified patient population.

Secondary objectives
  • To compare the disease control rate (DCR, defined as the proportion of patients with a best overall response of complete response, partial response, or stable disease which lasted at least 24 weeks) of nilotinib and imatinib in the above specified patient population.
  • To compare the time to treatment failure (TTF) of nilotinib and imatinib.
  • To compare the overall survival (OS) of nilotinib and imatinib.
  • To compare time to progression (TTP), response rate (RR), time to tumor response, and assess duration of response of nilotinib and imatinib (RECIST criteria).
  • To compare the safety and tolerability of nilotinib and imatinib.
  • To evaluate inter- and intra-patient variability in nilotinib and imatinib exposure over time, and to explore any relationship between the pharmacokinetic exposure of nilotinib or imatinib and clinical responses. (M. D. Anderson Cancer Center has opted out and will not participate in the pharmacokinetic testing portion of this protocol).

Exploratory objectives
  • To evaluate tumor response and PFS using Choi criteria, and compare these results with tumor response and PFS assessed by RECIST criteria.
  • To explore any relationship between tumor response and KIT and PDGFR mutations.
  • To explore whether individual variations in genetic and/or genomic characteristics confer differential response to nilotinib and imatinib, and possibly correlate to disease severity and progression (pharmacogenetic and pharmacogenomic assessment).
.
Study Status Information
Study Activation / Registration Date:05/11/2009
IRB Review and Approval Date:12/29/2008
Study Type:Phase Iii
Recruitment Status:Closed
Projected Accrual:736
.
Enrollment Eligibility
If you do not meet the enrollment eligibility, there may be other treatment options for you. Please Contact the Referral Office for more information.

Inclusion Criteria:1) Age >/=18 years

2) At least one measurable site of disease on CT/MRI scan as defined by RECIST criteria based on investigator's assessment

3) Histologically confirmed diagnosis of GIST which is unresectable and/or metastatic and either:---have not received any prior anti-neoplastic therapy other than adjuvant imatinib. Note:newly diagnosed patients may have received up to 14 days of treatment with imatinib for disease management while awaiting entry to the study or---had no clinical or radiological evidence of disease during the adjuvant treatment with imatinib, have recurrent GIST >/= 6 months after stopping adjuvant treatment with imatinib, and who have subsequently not received any other therapies,

4) Continued from #3 - For patients with recurrent GIST after stopping adjuvant imatinib two CT scans will be required prior to study entry:one demonstrating absence of disease following completion of adjuvant imatinib and another demonstrating recurrence of disease >/= 6 months after discontinuation of adjuvant imatinib.

5) WHO Performance Status of 0,1 or 2

6) Patients must have normal organ, electrolyte, and marrow function as defined by:Absolute Neutrophil Count (ANC) >/= 1.5 x 10^9/L, Hemoglobin >/= 9.0 g/dL,Platelets >/= 100 x 10^9/L, ALT and AST </=2.5 x upper limit of normal (ULN) or </= 5.0 x ULN if considered due to liver metastases, Alkaline phosphatase </= 2.5 x ULN or </= 5.0 x ULN if considered due to liver metastases,Serum bilirubin </= 1.5 x ULN, Serum lipase and amylase </= 1.5 x ULN, Serum potassium within the normal limits or corrected to within normal limits with supplements

7) Continued from #6 - Total calcium (corrected for serum albumin) within the normal limits or corrected to within normal limits with supplements, Serum magnesium within the normal limits or corrected to within normal limits with supplements, Serum phosphorous within the normal limits or corrected to within normal limits with supplements, Serum creatinine </= 1.5 x ULN. A written informed consent must be obtained

Exclusion Criteria:1) Any prior anti-neoplastic therapy (eg TKIs, chemotherapy, investigational therapy) with the exception of patients who have received adjuvant imatinib or patients with newly diagnosed metastatic/unresectable GIST whose disease requires therapy while awaiting entry to the study, up to 14 days of treatment with imatinib (a washout period of a minimum of 4 days will be required prior to the first dose of study medication).

2) History of active malignancy (other than GIST) within 10 years prior to study entry with the exception of previous or concomitant basal cell skin cancer, previous cervical carcinoma in situ

3) Impaired cardiac function, including any one of the following: LVEF < 45% or below the institutional lower limit of the normal range (whichever is higher) as determined by echocardiogram or MUGA scan, Inability to determine the QT interval on ECG, Complete left bundle branch block, Use of a ventricular-paced pacemaker, Congenital long QT syndrome or a known family history of long QT syndrome, History of or presence of clinically significant ventricular or atrial tachyarrhythmias, Clinically significant resting bradycardia (< 50 beats per minute).

4) Continued from #3 - QTc > 450 msec (using the QTcF formula) as determined by central reading, If QTcF > 450 msec and electrolytes are not within normal ranges, electrolytes should be corrected and then the patient re-screened for QTc, History or signs of prior myocardial infarction (during the last 12 months), History of unstable angina (during the last 12 months), Other clinically significant heart disease (e.g. congestive heart failure or uncontrolled hypertension).

5) Severe and/or uncontrolled concurrent medical disease that in the opinion of the investigator could cause unacceptable safety risks or compromise compliance with the protocol e.g. uncontrolled diabetes, active or uncontrolled infection.

6) History of significant congenital or acquired bleeding disorder unrelated to cancer.

7) Known symptomatic brain metastases.

8) Major surgery within 4 weeks prior to randomization or who have not recovered from prior surgery.

9) History of non-compliance to medical regimens or inability to grant consent.

10) Patients who are currently receiving treatment with any medications that have the potential to prolong the QT interval and the treatment cannot be either safely discontinued or switched to a different medication prior to starting study drug administration.

11) Patients actively receiving therapy with strong CYP3A4 inhibitors and the treatment cannot be either discontinued or switched to a different medication prior to starting study drug.

12) Patients actively receiving therapy with strong CYP3A4 inducers and the treatment cannot be either discontinued or switched to a different medication prior to starting study drug.

13) Patients actively receiving therapy with herbal medicines that are CYP3A4 inhibitors and/or inducers, and the treatment cannot be either discontinued or switched to a different medication prior to starting study drug. These herbal medicines may include Echinacea, (including E. purpurea, E. angustifolia and E. pallida), Piperine, Artemisinin, St. John's Wort, and Ginkgo.

14) Impairment of gastrointestinal (GI) function or GI disease that may significantly alter the absorption of study drug (e.g., ulcerative disease, uncontrolled nausea, vomiting, diarrhea, malabsorption syndrome), except for gastrectomy.

15) History of acute pancreatitis within 1 year of study entry or past medical history of chronic pancreatitis.

16) Acute or chronic uncontrolled liver, or severe renal disease considered unrelated to disease.

17) Patients who have received wide field radiotherapy within 4 weeks or limited field radiation for palliation within 2 weeks prior to randomization or who have not recovered from side effects of such therapy

18) Women who are a) pregnant, b) breast feeding c) of childbearing potential without a negative pregnancy test prior to baseline and (d) female of childbearing potential unwilling to use contraceptive precautions throughout the trial (post menopausal women must be amenorrheic for at least 12 months to be considered of non-childbearing potential.)

.
Links
Registration Number: NCT00785785
Study Information on Clinical Trials Registry (clinicaltrials.gov)

Other Links:
.
Results


Return to Clinical Trials at M.D. Anderson Cancer Center