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Study Summary
No. 2010-0049:.......Thyroid......Naifa L. Busaidy......Endocrine Neoplasia & Hormonal Disorders
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Study Summary Title
Study Summary
Number:
2010-0049
Study Title:A phase II trial using RAD001 for patients with radioiodine refractory thyroid cancer
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Physician New Patient Referral
Name:Naifa L. BusaidyPatients Call:800-392-1611 (in U.S.A.) 713-792-6161 (outside U.S.A.)
Dept:Endocrine Neoplasia & Hormonal DisordersReferring MD
Call:
800-392-1611 (in U.S.A.) 713-792-6161 (outside U.S.A.)
Phone:713-792-2841
Contact us about clinical trials
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General Information
Disease Group:ThyroidSupported By:Novartis
Phase of Study:Phase IIReturn
Visit:
A treatment cycle consists of 28 days.
Treatment
Agents:
RAD001Home Care:RAD001 should be taken by the patient in a fasting state or with no more than a
light fat-free meal. A dose of RAD001 is considered missed if the patient did
not take RAD001 within 6 hours of the scheduled time.
Treatment Loc:Both at MDACC & outside MDACC at one or more Collaborating Sites or Institutions
Estimated
Length of Stay
in Houston:
0 days, unless pt gets sick and needs hospitalization for other reasons.
Description/
Intervention:
The goal of this clinical research study is learn if RAD001 can help to control
locally-advanced or metastatic thyroid cancer. The safety of this drug will
also be studied.
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Study Objectives / Outcomes
Primary: Measure progression free survival in patients with progressive thyroid cancer

Secondary:
a. Objective response rate (complete and partial responses modified by RECIST criteria)
b. 1 year overal survival in patients with progressive thyroid cancer
c. Symptom improvement in medullary thyroid cancer cohort
d. To determine genetic expression of AKT, PTEN, PI3K, and analysis of mutations such as B-raf on tumor tissue.
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Study Status Information
Study Activation / Registration Date:
IRB Review and Approval Date:01/24/2011
Study Type:Phase Ii Or Phase I/Ii
Recruitment Status:Open
Projected Accrual:50 (33 DTC/ 10MTC/ 7anaplastic)
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Enrollment Eligibility
If you do not meet the enrollment eligibility, there may be other treatment options for you. Please Contact the Referral Office for more information.

Inclusion Criteria:1) Histologically confirmed locally advaced or metastatic thyroid cancer, excluding thyroid lymphomas not amenable to or refractory to surgical resection, external beam radiotherapy, radioiodine or other local therapies

2) Medullary thyroid cancer with documented evidence of disease progression by modified RECIST^34 within 6 months during the year prior to study day 1 ( or symptomatic disease (ie, medullary thyroid cancer-related diarrhea and /or flushing episodes) at the time of screening in the absence of documented disease progression.The patient must not have had any treatment between the date of progression and the start date of RAD001 treatment, unless discussed with the principal investigator (PI).

3) Differentated thyroid cancer (papillary, follicular with subvariants such as Hurthle cell thyroid cancer) with documented evidence of disease progression by modified RECIST within 6 months during the year prior to study day. The patient must not have had any treatment between the date of progression and the start date of RAD001 treatment, unless discussed with the PI.

4) Anaplastic thyroid cancer with disease progression with documented disease progression by modified RECIST within 6 months during the year prior to study day 1. The patient must not have had any treatment between the date of progression and the start date of RAD001 treatment, unless discussed with the PI.

5) Patients must have at least one measurable site of disease according to RECIST criteria that has not been previously irradiated. If the patient has had previous radiation to the marker lesion(s), there must be evidence of progression since the radiation

6) Age >/= 18 years

7) ECOG performance status </=2

8) Adequate bone marrow function as shown by: ANC >/= 1.5 x 10^9/L, Platelets >/= 100 x 10^9/L, Hb >9 g/dL

9) Adequate liver function as shown by:

10) Serum bilirubin </= 1.5 x ULN

11) International Normalized Ratio < 1.3 (or < 3 on anticoagulants)

12) ALT and AST </= 2.5x ULN (</= 5x ULN in patients with liver metastases)

13) Adequate renal function: serum creatinine </= 1.5 x ULN

14) Fasting serum cholesterol </=300 mg/dL OR </=7.75 mmol/L AND fasting triglycerides </= 2.5 x ULN.

15) Signed informed consent

Exclusion Criteria:1) Patients receiving anticancer therapies within last 2 weeks or who have received radiation therapy within 3 weeks of study day 1

2) Patients, who have had a major surgery or significant traumatic injury within 4 weeks of start of study drug, patients who have not recovered from the side effects of any major surgery (defined as requiring general anesthesia) or patients that may require major surgery during the course of the study

3) Prior treatment with any investigational drug within the preceding 3 weeks

4) Patients receiving chronic, systemic treatment with corticosteroids or another immunosuppressive agent. Topical or inhaled corticosteroids are allowed.

5) Patients should not receive immunization with attenuated live vaccines within 2 weeks of study entry or during study period

6) Patients who have brain or leptomeningeal metastases that can not be controlled with radiotherapy or radioiodine treatment including patients who require glucocorticoids for brain or leptomeningeal metastases.

7) Other malignancies within the past 3 years except for adequately treated carcinoma of the cervix or basal or squamous cell carcinomas of the skin. Exceptions may be made by the PI for other low risk cancer diagnosis within the last 3 years.

8) Patients who have any severe and/or uncontrolled medical conditions or other conditions that could affect their participation in the study such as:New York Heart Association Class III or IV; unstable angina pectoris, symptomatic congestive heart failure, myocardial infarction within 6 months of start of study drug, serious uncontrolled cardiac arrythmia or any other significat cardiac disease; severly imparied lung function; uncontrolled diabetes fasting serum >1.5xULN; active or uncontrolled severe infections; liver disease such as cirrhosis, chronic active or presistent hepatitis, positive screening hepatitis C test or history of HCV infection including those with a negative viral load test at baseline

9) A known history of HIV seropositivity

10) Impairment of gastrointestinal function or gastrointestinal disease that may significantly alter the absorption of RAD001 (e.g., ulcerative disease, uncontrolled nausea, vomiting, malabsorption syndrome or small bowel resection)

11) Patients with an active, bleeding diathesis

12) Female patients who are pregnant or breast feeding, or adults of reproductive potential who are not using effective birth control methods. If barrier contraceptives are being used, these must be continued throughout the trial by both sexes. Hormonal contraceptives are not acceptable as a sole method of contraception. (Women of childbearing potential must have a negative urine or serum pregnancy test within 14 days prior to administration of RAD001)

13) Patients who have received prior treatment with an mTOR inhibitor (sirolimus, temsirolimus, everolimus).

14) Patients with a known hypersensitivity to RAD001 (everolimus) or other rapamycins (sirolimus, temsirolimus) or to its excipients

15) History of noncompliance to medical regimens

16) Patients unwilling to or unable to comply with the protocol

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Links
Registration Number: NCT00936858
Study Information on Clinical Trials Registry (clinicaltrials.gov)

Other Links:
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Results


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