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Study Summary
No. 2010-0244:.......Leukemia; Myeloma......Elias Jabbour......Leukemia
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Study Summary Title
Study Summary
Number:
2010-0244
Study Title: A Phase 1 Dose - Escalation and Pharmacokinetic Study of TG02 Citrate in Patients with Advanced Hematological Malignancies
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Physician New Patient Referral
Name:Elias JabbourPatients Call:800-392-1611 (in U.S.A.) 713-792-6161 (outside U.S.A.)
Dept:LeukemiaReferring MD
Call:
800-392-1611 (in U.S.A.) 713-792-6161 (outside U.S.A.)
Phone:713-792-7305
Contact us about clinical trials
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General Information
Disease Group:Leukemia
Myeloma
Supported By:Tragara Pharmaceuticals, Inc.
Phase of Study:Phase IReturn
Visit:
Treatment
Agents:
TG02Home Care:
Treatment Loc:Both at MDACC & and Other Sites
Estimated
Length of Stay
in Houston:
Description/
Intervention:
The goal of this clinical research study is to find the highest tolerable dose
and schedule of TG02 citrate that can be given to patients with certain types
of leukemia, MDS, and CML. The safety of this drug will also be studied.
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Study Objectives / Outcomes
Primary Objective

The primary objective is to determine the DLT, MTD, and RP2D of TG02 citrate. Any schedule, if completed to MTD and planned for further evaluation in Phase 2 studies, will be expanded to a total of 12 patients at the MTD to obtain further safety and PK data.

Secondary Objectives

The secondary objectives are to:
  • Assess the safety and tolerability of TG02 citrate
  • Assess the PK profile of TG02 citrate
  • Evaluate exploratory biomarkers for TG02 citrate including pathway inhibition and the presence of polymorphisms of genes involved in the metabolism of TG02 citrate
  • Evaluate early evidence of anti-tumor activity as assessed by objective response (OR) and progression free survival (PFS)
  • Assess overall survival (OS)
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Study Status Information
Study Activation / Registration Date:
IRB Review and Approval Date:09/14/2010
Study Type:Phase I
Recruitment Status:Terminated
Projected Accrual:80-120
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Enrollment Eligibility
If you do not meet the enrollment eligibility, there may be other treatment options for you. Please Contact the Referral Office for more information.

Inclusion Criteria:1) Patients with the following histologically confirmed relapsed hematological malignancies for whom no curative treatment or standard therapy that conveys clinical benefit is available: AML; ALL; CML currently in blast crisis (defined as >/=30% blasts in bone marrow); High-risk MDS such as RAEB-1, RAEB-2, RAEB-T, and CMML

2) Elderly patients(>/= 65 years of age) with AML who are not eligible for standard frontline chemotherapy or who refuse treatment with intensive therapy are eligible.

3) The interval from prior treatment to time of study drug administration should be at least 5 half-lives for cytotoxic and noncytotoxic agents. If the patient is on hydroxyurea to control peripheral blood leukemic cell counts, the patient may remain on hydroxyurea until 24 hours prior to the first dose of study drug.

4) Persistent clinically significant toxicities from prior chemotherapy must be </=Grade 1.

5) >/=18 years of age.

6) Eastern Clinical Oncology Group Performance Status (ECOG PS) of 0, 1, or 2.

7) Laboratory values within the following ranges: Creatinine (Cr) </=2 X the upper limit of normal (ULN); ALT and/or AST </=2.5 X the ULN; Total bilirubin </=1.5 X the ULN, unless considered due to Gilbert's syndrome

8) Negative serum or urine pregnancy test at the time of first dose for women of childbearing potential (WOCBP). For men and WOCBP, adequate contraception must be used throughout the study. For this study, acceptable methods of contraception include a reliable intrauterine device or a spermicide in combination with a barrier method. Hormonal forms of birth control (oral, implantable, or injectable) may only be used if combined with another highly effective form of birth control such as a spermicide combined with a barrier method.

9) Ability to understand the requirements of the study, provide written informed consent and authorization of use and disclosure of protected health information, and agree to abide by the study restrictions and return for the required assessments.

10) Ability to take oral medication.

11) Inclusion Criteria for Multiple Myeloma

12) Patients with relapsed multiple myeloma. Patients must have received at least one line of therapy, must have progressed after at least one prior therapy, and be patients for whom no standard therapy is available or who decline such options. Prior autologous and/or allogeneic transplant is permitted.

13) Patients must have measurable disease (within 14 days prior to enrollment) defined as at least one of the following: Serum monoclonal protein (M protein) >/=500 mg/dL; Urine monoclonal protein >/=200 mg per 24 hours; Involved free light chain level >/=10 mg/dL (>/=100 mg/L) and an abnormal free light chain ratio in serum (<0.26 or >1.65); Measurable soft tissue (not bone) plasmacytoma (should be measured within 28 days of first dose of study drug)

14) Persistent clinically significant toxicities from prior chemotherapy must be </=Grade 1.

15) >/=18 years of age.

16) ECOG PS of 0, 1, or 2.

17) Laboratory values within the following ranges: Absolute neutrophil count of >/=1000/mm3; Platelet count of >/=50,000/mm3; Creatinine </=2 X the ULN; ALT and/or AST </=2.5 X the ULN; Total bilirubin <1.5 X the ULN, unless considered due to Gilbert's syndrome

18) Negative serum or urine pregnancy test at the time of first dose for WOCBP. For men and WOCBP, adequate contraception must be used throughout the study. For this study, acceptable methods of contraception include a reliable intrauterine device or a spermicide in combination with a barrier method. Hormonal forms of birth control (oral, implantable, or injectable) may only be used if combined with another highly effective form of birth control such as a spermicide combined with a barrier method.

19) Ability to understand the requirements of the study, provide written informed consent and authorization of use and disclosure of protected health information, and agree to abide by the study restrictions and return for the required assessments.

20) Ability to take oral medication.

Exclusion Criteria:1) Exclusion Criteria below are for all patients.

2) History of ventricular arrhythmia or symptomatic conduction abnormality within 12 months.

3) Previous allogenic hematopoietic transplant within 90 days of study enrollment

4) Concurrent severe or uncontrolled medical disease (i.e., active systemic infection, diabetes, hypertension, coronary artery disease, congestive heart failure) that, in the opinion of the Investigator, would compromise the safety of the patient or compromise the ability of the patient to complete the study.

5) Patients with prolonged QTc interval >450 ms as calculated by the Fridericia correction formula. Patients will be excluded if the calculation shows a >450 ms QTc interval prolongation.

6) Symptomatic CNS metastases. Patients with asymptomatic CNS disease may receive standard intrathecal chemotherapy prior to enrollment and continue once dosed with study drug.

7) Known human immunodeficiency virus or acquired immune deficiency syndrome.

8) Patients being actively treated for a second malignancy.

9) Pregnant or nursing women.

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Links
Registration Number: NCT01204164
Study Information on Clinical Trials Registry (clinicaltrials.gov)

Other Links:
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Results


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