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Study Summary
No. 2010-0257:.......Colorectum......Cathy Eng......Gastrointestinal Medical Oncology
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Study Summary Title
Study Summary
Number:
2010-0257
Study Title:A Phase III Randomized Double-Blind Study to Assess the Efficacy
and Safety of Perifosine Plus Capecitabine Versus Placebo Plus
Capecitabine in Patients with Refractory Advanced Colorectal
Cancer (Perifosine 343)
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Physician New Patient Referral
Name:Cathy EngPatients Call:800-392-1611 (in U.S.A.) 713-792-6161 (outside U.S.A.)
Dept:Gastrointestinal Medical OncologyReferring MD
Call:
800-392-1611 (in U.S.A.) 713-792-6161 (outside U.S.A.)
Phone:713-792-2828
Contact us about clinical trials
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General Information
Disease Group:ColorectumSupported By:Keryx / AOI Pharmaceuticals, Inc.
Phase of Study:Phase IIIReturn
Visit:
Treatment
Agents:
Capecitabine
Perifosine
Home Care:
Treatment Loc:Both at MDACC & and Other Sites
Estimated
Length of Stay
in Houston:
Description/
Intervention:
The goal of this clinical research study is to learn if the combination of
perifosine (also called the study drug) and Xeloda® (capecitabine) can help to
control advanced colorectal cancer. The safety of this combination treatment
will also be studied.
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Study Objectives / Outcomes
Primary Objective:
To compare overall survival (OS) of perifosine plus capecitabine vs. placebo plus capecitabine in patients with refractory advanced colorectal cancer. The study is considered a success if perifosine plus capecitabine can demonstrate a statistically significant improvement over placebo plus capecitabine at the two-sided 0.05 significance level for OS.

Secondary Objectives:
To 1) compare perifosine plus capecitabine vs. placebo plus capecitabine with respect to overall response rate (ORR = complete response (CR) + partial response (PR)), progression free survival (PFS), and time to progression (TTP) in patients with refractory advanced colorectal cancer; and 2) to evaluate the safety of the combination of perifosine plus capecitabine compared to placebo plus capecitabine.

Tertiary Objectives:
1) assess the relationship between perifosine disposition and patient covariates (population pharmacokinetics) utilizing a sparse sampling technique from the first 150 patients that agree to participate (with informed consent), and 2) explore the relationship of biomarkers in baseline archived paraffin and optional pre- and on-treatment blood and plasma, peripheral blood mononuclear cell (PBMC's), and fresh tumor biopsy samples to efficacy of treatment. The optional studies may be performed in up to 200 patients (who agree to participate with informed consent) at select centers.
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Study Status Information
Study Activation / Registration Date:02/17/2011
IRB Review and Approval Date:02/17/2011
Study Type:Phase Iii
Recruitment Status:Closed
Projected Accrual:430
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Enrollment Eligibility
If you do not meet the enrollment eligibility, there may be other treatment options for you. Please Contact the Referral Office for more information.

Inclusion Criteria:1) Patients with histologically (or cytologically) confirmed adenocarcinoma of the colon or rectum that is recurrent or metastatic.

2) Patients must have failed available therapy for the treatment of advanced colorectal cancer. This is defined as progressive disease during or within 6 months after fluoropyrimidine, irinotecan, oxaliplatin, bevacizumab, and for K-ras wild-type (WT) patients, anti-EGFR antibody (cetuximab or panitumumab) containing therapies, with most recent progression by RECIST criteria. Patients who had at least stable disease as best response on their prior therapies (listed above) should have received at least 2 months (approximately 60 days) of treatment. For oxaliplatin-based therapy, failure of therapy will also include patients who progressed within 12 months of adjuvant therapy and patients who had oxaliplatin stopped secondary to toxicity.

3) Patients must have K-Ras status testing results available or a tumor tissue sample available for K-Ras testing.

4) Patients must have at least one measurable lesion by RECIST criteria.

5) No prior exposure to capecitabine in the metastatic colorectal cancer setting, except limited-course radiosensitizing capecitabine (capecitabine given concurrently with radiation therapy for no more than 30 radiation treatment days), which will be allowed in the metastatic setting. Previous capecitabine use in the neo-adjuvant and/or adjuvant setting is allowed as long as 12 months elapsed between the last neo-adjuvant and/or adjuvant capecitabine dose and diagnosis of recurrent and/or metastatic disease.

6) Patient has an Eastern Cooperative Oncology Group (ECOG) performance status of 0 to 1 inclusively.

7) Patients must have adequate organ and marrow function as outlined below: ANC >/= 1500, Platelets >/= 75,000, HGB >/= 9 (with or without growth factor support), Creatinine </= 2.0 mg/dl, total, bilirubin </= 1.5x upper limit of normal, transaminase (ALT/AST) </= 2.5x upper limit of normal (</= 5x upper limit of normal in patients with liver metastases)

8) Patients must have recovered from acute toxicity or reached a new chronic stable baseline related to prior therapy excluding alopecia.

9) Patients must be able to ingest oral medications and have no known impairment of gastrointestinal function that is of the investigator's opinion would alter drug absorption.

10) Patients must be an adult (age >/= 18 years at the time of signing informed consent document or on the randomization date).

11) Patients must have ability to understand and the willingness to sign a written informed consent document.

12) Patient must be able to adhere to the study visit schedule and other protocol requirements.

13) All necessary baseline studies for determining eligibility must be obtained within 14 days prior to enrollment. (Pregnancy test must be within 72 hours for women of childbearing potential.). All patients will have a baseline evaluation that includes a chest, abdomen, and pelvic CT or MRI scan ideally within 14 days but no more than 28 days prior to starting treatment.

14) Women of child-bearing potential (WCBP), defined as a sexually mature woman who has not undergone a hysterectomy or who has not been naturally postmenopausal for at least 24 consecutive months (i.e., who has had menses any time in the preceding 24 consecutive months), must have a negative serum pregnancy test within 72 hours prior to enrollment. In addition, each sexually active WCBP and male patient must agree to use adequate contraceptive methods (oral, injectable, or implantable hormonal contraceptive; tubal ligation; intra-uterine device; barrier contraceptive with spermicide; or vasectomized partner) throughout the study for 4 weeks after the completion of treatment..

Exclusion Criteria:1) Patients with prior exposure to perifosine.

2) Patients receiving any other investigational agents or devices within three weeks (21 days) prior to Cycle 1 Day1.

3) History of allergic reactions attributed to compounds of similar chemical or biologic composition to perifosine (miltefosine or edelfosine).

4) Patients with known dipyrimidine dehydrogenase (DPD) deficiency or prior severe reaction to 5-FU.

5) Chemotherapy or other therapy experimental or proven that is or may be active against advanced colorectal cancer within three weeks (21 days) prior to Cycle 1 Day 1.

6) Patients who have had a major surgical procedure, open biopsy, or significant traumatic injury </=4 weeks prior to Cycle 1 Day 1.

7) Patients with a serious non-healing wound, active ulcer, or untreated bone fracture.

8) History of other carcinomas within the last five years, except cured non-melanoma skin cancer, curatively treated in-situ cervical cancer, or localized prostate cancer with a current PSA of <1.0 mg/dL on 2 successive evaluations, at least 3 months apart, with the most recent evaluation no more than 4 weeks prior to day 1 of the study drug treatment.

9) Patients with known central nervous system CNS metastases. Patients with CNS metastases that have been treated and are stable and who do not require corticosteroid treatment for the metastases (off steroids > 2 weeks) will be allowed.

10) Patients with known HIV, Hepatitis B, or Hepatitis C seropositivity.

11) Uncontrolled intercurrent illness including, but not limited to, ongoing or active infection and psychiatric illness/social situations that would limit compliance with study requirements.

12) Patients with a history of unstable or newly diagnosed angina pectoris, recent myocardial infarction (within 6 months of enrollment), or New York Heart Association class II-IV congestive heart failure.

13) Female patients who are pregnant or lactating are ineligible. All females of childbearing potential must have a negative serum pregnancy test within 72 hours of treatment. Men and women of childbearing potential must agree to employ adequate contraception to prevent pregnancy while on therapy and for 4 weeks after the completion of treatment.

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Links
Registration Number: NCT01097018
Study Information on Clinical Trials Registry (clinicaltrials.gov)

Other Links:
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Results


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