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Study Summary
No. 2011-0035:.......Thyroid......Mouhammed A. Habra......Endocrine Neoplasia & Hormonal Disorders
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Study Summary Title
Study Summary
Number:
2011-0035
Study Title:A Multicenter, Randomized, Double-Blind, Placebo-Controlled, Phase 3 Trial of E7080 in 131I-Refractory Differentiated Thyroid Cancer
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Physician New Patient Referral
Name:Mouhammed A. HabraPatients Call:800-392-1611 (in U.S.A.) 713-792-6161 (outside U.S.A.)
Dept:Endocrine Neoplasia & Hormonal DisordersReferring MD
Call:
800-392-1611 (in U.S.A.) 713-792-6161 (outside U.S.A.)
Phone:713-792-2841
Contact us about clinical trials
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General Information
Disease Group:ThyroidSupported By:Eisai
Phase of Study:Phase IIIReturn
Visit:
Treatment
Agents:
E7080Home Care:
Treatment Loc:Both at MDACC & and Other Sites
Estimated
Length of Stay
in Houston:
Description/
Intervention:
Unavailable
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Study Objectives / Outcomes
Primary Objective:
  • To compare the Progression-free Survival (PFS) of subjects with 131I-refractory differentiated thyroid cancer (DTC) with radiographic evidence of disease progression within the prior 12 months treated with E7080 versus Placebo.
Secondary Objectives:
  • To compare Overall Response Rate (ORR) (Complete and Partial Responses, CR and PR) of subjects treated with E7080 versus Placebo.
  • To compare Overall Survival of subjects treated with E7080 versus Placebo.
  • To compare safety and tolerability of E7080 versus Placebo.
  • To assess the pharmacokinetic (PK) profile of E7080 in subjects with DTC.
Exploratory Objectives:
  • To compare Disease Control rate (DCR) (CR + PR + stable disease [SD]), Clinical Benefit Rate (CBR) (CR, PR + durable SD) and durable SD (SD >/= 23 weeks) of subjects treated with E7080 versus Placebo.
  • To assess safety and efficacy of E7080 administered in the Optional Open Label E7080 Treatment Period
  • To identify and validate blood and tumor biomarkers which correlate with efficacy-related endpoints of this study
  • To identify and validate DNA-sequence variants in genes influencing E7080 absorption, distribution, metabolism, excretion (ADME)
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Study Status Information
Study Activation / Registration Date:09/23/2011
IRB Review and Approval Date:09/23/2011
Study Type:Phase Iii
Recruitment Status:Closed
Projected Accrual:360
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Enrollment Eligibility
If you do not meet the enrollment eligibility, there may be other treatment options for you. Please Contact the Referral Office for more information.

Inclusion Criteria:1) Subjects must have histologically or cytologically confirmed diagnosis of one of the following DTC subtypes: a. Papillary thyroid cancer (PTC) i. Follicular variant ii. Variants (including but not limited to tall cell, columnar cell, cribriform-morular, solid, oxyphil, Warthin's-like, trabecular, tumor with nodular fasciitis-like stroma, Hürthle cell variant of papillary carcinoma, poorly differentiated) b. Follicular thyroid cancer (FTC) i. Hürthle cell ii. Clear cell iii. Insular

2) Measurable disease meeting the following criteria and confirmed by central radiographic review: a. At least one lesion of >/= 1.0 cm in the longest diameter for a non-lymph node or >/= 1.5 cm in the short-axis diameter for a lymph node which is serially measurable according to RECIST 1.1 using computed tomography / magnetic resonance imaging (CT/MRI). If there is only one target lesion and it is a non-lymph node, it should have a longest diameter or >/=1.5cm. b. Lesions that have had external beam radiotherapy (EBRT) or loco-regional therapies such as radiofrequency (RF) ablation must show evidence of progressive disease based on RECIST 1.1 to be deemed a target lesion

3) Subjects must show evidence of disease progression within 12 months (an additional month will be allowed to accommodate actual dates of performance of scans, i.e., within </=13 months) prior to signing informed consent, according to RECIST 1.1 assessed and confirmed by central radiographic review of CT and / or MRI scans

4) Subjects must be 131^I-refractory / resistant as defined by at least one of the following : a. One or more measurable lesions that do not demonstrate 131^I uptake on any radioiodine scan b. One or more measurable lesions that has progressed by RECIST 1.1 within 12 months of 131^I therapy, despite demonstration of radioiodine avidity at the time of that treatment by pre- or post-treatment scanning These subjects must not be eligible for possible curative surgery. c. Cumulative activity of 131^I of > 600 mCi or 22 gigabequerels (GBq), with the last dose administered at least 6 months prior to study entry

5) Subjects may have received 0 or 1 VEGF/VEGFR-targeted therapy (ex: sorafenib, sunitinib, pazopanib, etc.)

6) Subjects with known brain metastases who have completed whole brain radiotherapy, stereotactic radiosurgery or complete surgical resection, will be eligible if they have remained clinically stable, asymptomatic and off of steroids for one month

7) Subjects must be receiving thyroxine suppression therapy and thyroid stimulating hormone (TSH) should not be elevated (TSH should be </= 5.50 mcu/mL). When tolerated by the subject, thyroxine dose should be changed to achieve TSH suppression (TSH < 0.50 mcu/mL) and this dose can be changed concurrently upon starting E7080

8) All chemotherapy or radiation-related toxicities must have resolved to < Grade 2 severity per CTCAE criteria v 4.0, except alopecia and infertility.

9) Subjects must have an Eastern Cooperative Oncology Group (ECOG) Performance Status of 0 - 2

10) Adequately controlled blood pressure with or without antihypertensive medications, defined as BP =/< 150/90 mm Hg at screening and no change in antihypertensive medications within 1 week prior to the Screening Visit

11) Adequate renal function defined as calculated creatinine clearance >/= 30 mL/min per the Crockcroft and Gault formula

12) Adequate bone marrow function: a. Absolute neutrophil count (ANC) >/= 1500/mm^3 (>/=1.5 × 10^3/μL); b. Platelets >/= 100,000/mm^3 (>/= 100 × 10^9/L); c. Hemoglobin >/= 9.0 g/dL.

13) Adequate blood coagulation function as evidenced by an International Normalized Ratio (INR) </= 1.5

14) Adequate liver function: a. Bilirubin </= 1.5 × the upper limit of normal (ULN) except for unconjugated hyperbilirubinemia or Gilbert's syndrome; b. Alkaline phosphatase, alanine aminotransferase (ALT), and aspartate aminotransferase (AST) </= 3 × the ULN (</= 5 × ULN if subject has liver metastases).

15) Males or females age >/= 18 years at the time of informed consent

16) Females must not be lactating or pregnant at Screening or Baseline (as documented by a negative beta human chorionic gonadotropin test with a minimum sensitivity of 25 IU/L or equivalent units of beta-hCG). A separate baseline assessment is required if a negative screening pregnancy test was obtained more than 72 hours before the first dose of study drug.

17) All females will be considered to be of childbearing potential unless they are postmenopausal (amenorrheic for at least 12 consecutive months, in the appropriate age group, and without other known or suspected cause) or have been sterilized surgically (i.e., bilateral tubal ligation, total hysterectomy, or bilateral oophorectomy, all with surgery at least 1 month before dosing)

18) Females of childbearing potential must not have had unprotected sexual intercourse within 30 days prior to study entry and must agree to use a highly effective method of contraception (e.g., total abstinence, an intrauterine device, a doublebarrier method [such as condom plus diaphragm with spermicide], a contraceptive implant, an oral contraceptive, or have a vasectomized partner with confirmed azoospermia) throughout the entire study period and for 30 days after study drug discontinuation. If currently abstinent, the subject must agree to use a double-barrier method as described above if she becomes sexually active during the study period or for 30 days after study drug discontinuation. Females who are using hormonal contraceptives must have been on a stable dose of the same hormonal contraceptive product for at least 4 weeks prior to dosing and must continue to use the same contraceptive during the study and for 30 days after study drug discontinuation

19) Male subjects must have had a successful vasectomy (confirmed azoospermia) or they and their female partners must meet the criteria above (i.e., not of childbearing potential or practicing highly effective contraception throughout the study period and for 30 days after study drug discontinuation) Those with partners using hormonal contraceptives must also be using an additional approved method of contraception, as described previously.

20) Voluntary agreement to provide written informed consent and the willingness and ability to comply with all aspects of the protocol.

Exclusion Criteria:1) Anaplastic or medullary carcinoma of the thyroid

2) Two or more prior VEGF / VEGFR-targeted therapies or any ongoing treatment for 131I-refractory DTC other than TSH-suppressive thyroid hormone therapy

3) Prior treatment with E7080

4) Subjects who have received any anticancer treatment within 21 days or any investigational agent within 30 days prior to the first dose of study drug and should have recovered from any toxicity related to previous anticancer treatment. This does not apply to the use of TSH-suppressive thyroid hormone therapy.

5) Major surgery within 3 weeks prior to the first dose of study drug

6) Subjects having > 1 + proteinuria on urine dipstick testing will undergo 24h urine collection for quantitative assessment of proteinuria. Subjects with urine protein >/= 1 g/24h will be ineligible

7) Gastrointestinal malabsorption, or any other condition in the opinion of the investigator that might affect the absorption of E7080

8) Significant cardiovascular impairment: history of congestive heart failure greater than New York Heart association (NYHA) Class II; unstable angina; myocardial infarction or stroke within 6 months of the first dose of study drug; or cardiac arrhythmia requiring medical treatment

9) Prolongation of QTcF interval to > 480 msec

10) Bleeding or thrombotic disorders or use of anticoagulants such as, warfarin or similar agents requiring therapeutic INR monitoring. (Treatment with Low molecular weight heparin (LMWH) is allowed.)

11) Active hemoptysis (bright red blood of at least 0.5 teaspoon) within 3 weeks prior to the first dose of study drug

12) Active infection (any infection requiring treatment)

13) Active malignancy (except for DTC or definitively treated melanoma in-situ, basal or squamous cell carcinoma of the skin, or carcinoma in-situ of the cervix) within the past 24 months

14) Known intolerance to any of the study drugs (or any of the excipients)

15) Any medical or other condition which, in the opinion of the investigator, would preclude participation in a clinical trial

16) Females who are pregnant or breastfeeding

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Links
Registration Number: NCT01321554
Study Information on Clinical Trials Registry (clinicaltrials.gov)

Other Links:
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Results


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