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Study Summary
No. 2011-0746:.......Brain; CNS......Charles A. Conrad......Neuro Oncology
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Study Summary Title
Study Summary
Number:
2011-0746
Study Title:A Phase I/Ib, open-label study in patients with recurrent glioblastoma to assess the safety and tolerability of macitentan in combination with dose-dense temozolomide.
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Physician New Patient Referral
Name:Charles A. ConradPatients Call:800-392-1611 (in U.S.A.) 713-792-6161 (outside U.S.A.)
Dept:Neuro OncologyReferring MD
Call:
800-392-1611 (in U.S.A.) 713-792-6161 (outside U.S.A.)
Phone:713-792-2883
Contact us about clinical trials
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General Information
Disease Group:Brain
CNS
Supported By:ACTELION Pharmaceuticals Ltd
Phase of Study:Phase IReturn
Visit:
Treatment
Agents:
Macitentan
Temozolomide
Home Care:
Treatment Loc:Only at MDACC
Estimated
Length of Stay
in Houston:
Description/
Intervention:
The goal of this clinical research study is to find the highest tolerable dose
of macitentan combined with temozolomide that can be given to patients with
glioblastoma or gliosarcoma. Researchers also want to learn how quickly the
study drug spreads through the body once it has been given. The safety of these
drugs given together will also be studied.

Macitentan is designed to block several proteins on the surface of the cells
that are important to the growth and division of cancer cells and the growth of
blood vessels, which may cause the cancer cells to die.

Temozolomide is designed to damage the DNA of cancer cells. The damaged DNA
may cause tumor cell death.
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Study Objectives / Outcomes
1. Primary objectives

    Phase 1 Dose Escalation period
  • To determine the Maximum tolerated dose (MTD) of macitentan (M) in combination with Dose-dense temozolomide (ddTMZ) in patients with recurrent Glioblastoma multiforme (GBM) or Gliosarcoma (GS).

    Phase 1b period
  • To expand the safety and tolerability database of the recommended macitentan and ddTMZ dosing schedule derived from the Phase 1 Dose Escalation Period.

    Ancillary Study
  • To evaluate the effects of macitentan on biomarkers in brain tumor tissue.

    2. Secondary objectives

    Phase 1 Dose Escalation period
  • To determine the safety and tolerability of different doses of macitentan in combination with ddTMZ.

    Phase 1b period
  • To explore the efficacy of the recommended macitentan and ddTMZ dosing schedule.

    Ancillary Study
  • To determine the safety and tolerability of two different doses of macitentan in combination with ddTMZ.

    All study periods
  • To evaluate the Pharmacokinetics (PK) of macitentan and its active metabolite ACT-132577 and TMZ and its metabolite active Metabolite of temozolomide (MTIC).
  • To evaluate the effects of macitentan on biomarkers in hair follicles.
  • To explore efficacy of each tested dose and schedule of macitentan combined with ddTMZ.
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Study Status Information
Study Activation / Registration Date:
IRB Review and Approval Date:01/11/2012
Study Type:Phase I
Recruitment Status:Open
Projected Accrual:N/A
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Enrollment Eligibility
If you do not meet the enrollment eligibility, there may be other treatment options for you. Please Contact the Referral Office for more information.

Inclusion Criteria:1) Signed informed consent prior to any study-mandated procedure.

2) Male or female patients >/= 18 years of age.

3) Patients with histologically confirmed GBM or GS.

4) Recurrent disease with an: 1) interval of >/= 3 months following radiotherapy + temozolomide; 2) interval of >/= 3 weeks between end of surgery and start of protocol therapy for patients who have undergone surgery for recurrent disease.

5) Patients who tolerated previous administration with temozolomide, including no requirement for blood product transfusions.

6) Karnofsky performance status (KPS) >/= 60%

7) Complete blood count (CBC)/differential at screening, with adequate bone marrow function as defined by: absolute neutrophil count (ANC) >/= 1,500/ul; platelets >/= 100,000/ul; hemoglobin >/= 10 g/dL.

8) If patient is receiving steroids, must be on stable or decreasing steroid dose within 5 days prior to treatment initiation with macitentan.

9) Patients must be willing to forego other cytotoxic and non-cytotoxic drug therapy against the tumor while enrolled in the study.

10) Women of childbearing potential must have a negative serum beta-Human chorionic gonadotropin (HCG) pregnancy test documented within 14 days prior to study initiation.

11) Women of childbearing potential must agree to use two reliable methods of contraception from screening and up to 30 days after discontinuation of study treatment. Reliable methods of contraception include intrauterine devices (IUD) or intrauterine systems (IUS), tubal sterilization, hormonal methods (combined or progesterone only oral contraceptives, transdermal patches, vaginal rings, injections, implants) and barrier methods (male condom, diaphragm, or cervical cap). A female partner's vasectomy still requires 1 additional method of contraception. Abstinence, the rhythm method, or contraception by the other partner alone, will not be considered as a reliable methods of contraception. Males not naturally or surgically sterile, who have a female partner of childbearing potential, must agree to use two reliable methods of contraception from screening and up to 30 days after discontinuation of study treatment

12) Ancillary Study: patients who need to undergo surgical resection for the recurrent glioblastoma and will be pre-treated with macitentan prior to surgery.

Exclusion Criteria:1) Histology other than astrocytoma grade IV (GBM or gliosarcoma)

2) Tumor foci detected below the tentorium or beyond the cranial vault.

3) Glioblastoma or gliosarcoma disease with leptomeningeal spread.

4) Patients with a history of any other cancer, unless in complete remission, and off all therapy for that disease for a minimum of 5 years (except history of basal or squamous cell skin cancers that are completely excised/cured at time of enrollment).

5) Serum aspartate aminotransferase (AST), alanine aminotransferase (ALT), or bilirubin greater than the upper limit of normal (ULN).

6) Moderate to severe hepatic impairment, i.e., Child-Pugh Class B/C.

7) Positive results from Human immunodeficiency virus (HIV) serology testing, if any available.

8) Supine systolic blood pressure < 100 mmHg or supine diastolic blood pressure < 50 mmHg at screening (Visit 1) and baseline (Visit 2), or documented medical history of orthostatic hypotension.

9) Renal insufficiency (estimated creatinine clearance < 50 mL/min, or serum creatinine exceeding laboratory ULN at screening).

10) Females who are pregnant or lactating or plan to become pregnant during the course of this study.

11) Substance or alcohol abuse or dependence, within 12 months prior to screening (Visit 1).

12) Treatment with endothelin receptor antagonists (ERAs) within 3 months prior to screening (Visit 1).

13) Treatment with cytochrome P450 3A4 (CYP3A4) inducers, such as rifabutin, rifampin, rifapentin, carbamazepine and derivates, phenobarbital, phenytoin, St. John's wort within 3 weeks prior to screening (Visit 1)

14) Treatment with strong CYP3A4 inhibitors such as ketoconazole, itroconazole, nefazodone, chloramphenicol, clarithromycin, telithromycin, ritonavir, indinavir, nelfinvar, and saquinavir within 2 weeks prior to screening (Visit 1).

15) Known hypersensitivity to endothelin receptor antagonists, or any of the excipients of macitentan tablets.

16) Prior chemotherapy for recurrent GBM with nitrosourea compounds including GliadelŪ (carmustine) wafers or bevacizumab.

17) Prior focal radiotherapy (stereotactic radiotherapy or Gamma Knife).

18) Planned treatment, or treatment with any investigational drug within 4 weeks prior to screening (Visit 1).

19) Severe, active co-morbidity, including: Cardiac disease - congestive heart failure class III/IV New York Heart Association (NYHA); unstable angina or new onset angina (began within the last 3 months) or myocardial infarction within the past 6 months; cardiac ventricular arrhythmias requiring anti-arrhythmic therapy; acute bacterial or fungal infection requiring intravenous antibiotics at the time of screening; chronic hepatitis B or C infection; chronic obstructive pulmonary disease exacerbation or other respiratory illness requiring hospitalization or precluding study therapy at the time of screening; hematological and bone marrow diseases. Severe malabsorption (defined as > 15% unintentional loss of body weight in the last 6 months prior to study enrollment).

20) Any condition that prevents compliance with the protocol or adherence to therapy.

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Links
Registration Number: NCT01499251
Study Information on Clinical Trials Registry (clinicaltrials.gov)

Other Links:
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Results


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