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Study Summary
No. 2011-0827:.......Leukemia......Guillermo Garcia-Manero......Leukemia
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Study Summary Title
Study Summary
Number:
2011-0827
Study Title:A Phase 1 Study of ARRY-614 in Patients with Low or Intermediate-1 Risk
Myelodysplastic Syndromes
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Physician New Patient Referral
Name:Guillermo Garcia-ManeroPatients Call:800-392-1611 (in U.S.A.) 713-792-6161 (outside U.S.A.)
Dept:LeukemiaReferring MD
Call:
800-392-1611 (in U.S.A.) 713-792-6161 (outside U.S.A.)
Phone:713-745-3428
Contact us about clinical trials
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General Information
Disease Group:LeukemiaSupported By:Array BioPharma
Phase of Study:Phase IReturn
Visit:
Treatment
Agents:
ARRY-614Home Care:
Treatment Loc:Both at MDACC & and Other Sites
Estimated
Length of Stay
in Houston:
Description/
Intervention:
The goal of this clinical research study is to learn the highest tolerable dose
of ARRY-614 that can be given to patients with MDS either 1 or 2 times a day.

ARRY-614 is designed to block the function of certain proteins that cause
normal blood cells to die in patients with MDS. This could cause the normal
blood cells to survive.
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Study Objectives / Outcomes
Primary Objectives
Determine the recommended Phase 2 schedule (QD or BID dosing) and dose of ARRY-614 administered as a semi-solid suspension (formulated) capsule in patients with low or intermediate-1 risk myelodysplastic syndromes (MDS).

Secondary Objectives
  • Obtain preliminary estimates of efficacy of ARRY-614
  • Explore potential markers for response in bone marrow and peripheral blood samples, as feasible
  • Assess possible PK/safety, PK/PD, PK/efficacy and PD/efficacy correlations
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Study Status Information
Study Activation / Registration Date:01/13/2012
IRB Review and Approval Date:01/13/2012
Study Type:Phase I
Recruitment Status:Open
Projected Accrual:82
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Enrollment Eligibility
If you do not meet the enrollment eligibility, there may be other treatment options for you. Please Contact the Referral Office for more information.

Inclusion Criteria:1) Provide a personally signed and dated informed consent document prior to initiation of any study-related procedures that are not considered standard of care.

2) Male or female >/= 18 years of age at time of signing consent.

3) Confirmed MDS by bone marrow biopsy according toWorld Health Organization (WHO) or FAB criteria.

4) Classification by the IPSS as low or intermediate-1 risk MDS according to cytogenetics, blood cytopenias and % bone marrow blasts within 6 weeks of the first dose of treatment in this study.

5) Patients may have received prior therapies for MDS. Newly diagnosed and previously untreated cases are also eligible if they require treatment and are not eligible for or refuse other treatment options.

6) Documented evidence of at least 1 of the following hematopoietic criteria : a. Hemoglobin </= 11 g/dL and/or RBC transfusion dependence (defined as requiring >/= 4 units of packed RBCs administered with a pretreatment hemoglobin value of </= 9 g/dL in the 8 weeks prior to first dose of treatment in this study). b. ANC </= 1.0 × 10^9/L. c. Platelet count </= 100 × 10^9/L or platelet transfusion dependence (defined as >/= 1 platelet transfusion administered with a pretreatment platelet value of </= 20 × 10^9/L in the 8 weeks prior to first dose of treatment in this study).

7) Eastern Cooperative Oncology Group (ECOG) performance status (PS) of 0, 1 or 2.

8) Adequate liver function: a. Total bilirubin </= 1.5 × the upper limit of normal (ULN), unless presence of Gilbert's Syndrome. b. AST and ALT </= 2.5 × ULN.

9) Adequate renal function: Serum creatinine </= 2 mg/dL or a calculated creatinine clearance of >/= 50 mL/min (using the Cockcroft and Gault method).

10) Male patients and female patients of childbearing potential must agree to use an effective method of contraception per institutional standard.

11) Willingness and ability to comply with scheduled visits, treatment plan, laboratory tests and other study procedures.

Exclusion Criteria:1) Receiving any treatment for MDS other than transfusions or a stable dose (>/= 4 weeks) of hematopoietic growth factors on study Day 1.

2) Treatment with any of the following: a. Azacitidine or decitabine: within 2 weeks prior to first dose of study treatment. b. Chronic use (> 2 weeks) of greater than physiologic doses of PO, subcutaneous (SC) or intravenous (IV) corticosteroids (dose equivalent to > 20 mg/day of prednisone): within 4 weeks prior to the first dose of study treatment. c. Immunomodulatory agent (e.g., lenalidomide): within 4 weeks prior to the first dose of study treatment.

3) History of a bone marrow transplant.

4) Concomitant malignancies or previous malignancies with less than a 2-year disease-free interval at the time of enrollment. Patients with adequately resected basal or squamous cell carcinoma of the skin, carcinoma in situ of the cervix, or Stage A low grade prostate cancer may enroll irrespective of the time of diagnosis.

5) Medical, psychiatric, cognitive or other conditions that may compromise the patient's ability to understand the patient information, to give informed consent, to comply with the study protocol, or to complete the study.

6) Any severe concurrent disease or condition (including active systemic infection, symptomatic congestive heart failure, unstable angina pectoris or cardiac arrhythmia) that, in the judgment of the Investigator, would make the patient inappropriate for study participation.

7) Patients with chronic myelomonocytic leukemia whose WBC count has been >/= 13.0 × 10^9/L at any point during the 8 weeks prior to the first dose of study drug.

8) Patients who require oral anticoagulants with coumarin derivates (e.g., warfarin, phenprocoumon), unless the patient is willing to allow for increased vigilance with respect to international normalized ratio (INR) testing per institutional monitoring practices.

9) 12-lead ECG demonstrating a QTcF of >/= 480 msec (mean of the triplicate ECG measurements) collected during Screening, with the exception of patients with atrioventricular pacemakers.

10) Significant GI abnormalities, including an inability to take oral medication, requirement for IV alimentation, active peptic ulcer, or prior surgical procedures affecting absorption.

11) Use of an investigational agent that is not expected to be cleared by the first dosing of study drug or that has demonstrated to have prolonged side effects. Patients should have recovered from the side effects to a Grade 0 or 1 (except alopecia).

12) Pregnant or lactating females.

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Links
Registration Number: NCT01496495
Study Information on Clinical Trials Registry (clinicaltrials.gov)

Other Links:
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Results


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