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Study Summary
No. 2012-0137:.......Lymphoma......Yasuhiro Oki......Lymphoma/Myeloma
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Study Summary Title
Study Summary
Number:
2012-0137
Study Title:A Phase 1 Study of IPI-145 in Patients with Advanced
Hematologic Malignancies
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Physician New Patient Referral
Name:Yasuhiro OkiPatients Call:800-392-1611 (in U.S.A.) 713-792-6161 (outside U.S.A.)
Dept:Lymphoma/MyelomaReferring MD
Call:
800-392-1611 (in U.S.A.) 713-792-6161 (outside U.S.A.)
Phone:713-792-2860
Contact us about clinical trials
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General Information
Disease Group:LymphomaSupported By:Infinity Pharmaceuticals, Inc.
Phase of Study:Phase IReturn
Visit:
Treatment
Agents:
IPI-145Home Care:
Treatment Loc:Both at MDACC & and Other Sites
Estimated
Length of Stay
in Houston:
Description/
Intervention:
The goal of this clinical research study is to learn about the safety of
IPI-145 and find the highest tolerable dose that can be given to patients with
advanced blood cancer.

IPI-145 is designed to block the normal signals in blood cells that tell the
cells to divide and grow. This may cause cancer cells to stop growing and/or
die.
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Study Objectives / Outcomes
The primary objectives of the study are:

• To determine the safety and the maximum tolerated dose (MTD) of IPI-145 in patients with advanced hematologic malignancies.
• To recommend a dose and schedule of IPI-145 for subsequent studies in patients with advanced hematologic malignancies.

The secondary objectives of the study are:
• To examine the pharmacokinetics of IPI-145 and, if applicable, its metabolite(s).
• To assess the potential biological activity of IPI-145 in hematologic malignancies.

The exploratory objective of the study is:
• To examine the relationship between various biological markers and the pharmacokinetics, safety and/or biological activity of IPI-145.

The primary endpoints of the study are:
• Incidence of reported adverse events and abnormal laboratory test results, including dose limiting toxicities (DLTs).

The secondary endpoints of the study are:
• Plasma concentrations of IPI-145 and, if applicable, its metabolite(s).
• Disease-specific response including, but not limited to, complete response (CR) and partial response.

The exploratory endpoints of the study are:
• Pharmacodynamic and predictive biomarkers within normal or malignant tissue or circulating cells or blood.
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Study Status Information
Study Activation / Registration Date:05/31/2012
IRB Review and Approval Date:05/31/2012
Study Type:Phase I
Recruitment Status:Open
Projected Accrual:250
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Enrollment Eligibility
If you do not meet the enrollment eligibility, there may be other treatment options for you. Please Contact the Referral Office for more information.

Inclusion Criteria:1) >/= 18 years of age at the time of signing the informed consent.

2) Life expectancy of at least 3 months.

3) For Dose Escalation/MTD Confirmation Only: Diagnosis of any advanced hematologic malignancy other than acute leukemia, CML in blast crisis and high risk or intermediate type; 2 myelodysplastic syndrome. For Expansion Cohort 1 Only: Diagnosis of INHL, MCL or CLL. For Expansion Cohort 2 Only: Diagnosis of mature cutaneous or non-cutaneous T cell lymphomas (excluding lymphoblastic lymphoma). At least 6 patients within each subtype of mature T-cell lymphoma must have tumors amenable to repeat biopsies and consent to at least two tumor biopsies. For Expansion Cohort 3 Only: Diagnosis of DLBCL or transformed follicular NHL. For Expansion Cohort 4 Only: Diagnosis of myeloproliferative neoplasms (myelofibrosis and all phases of CML), AML, MDS (including intermediate and high risk). For Expansion Cohort 5 Only: Diagnosis of acute lymphocytic leukemia/lymphoblastic lymphoma (T-cell or B-cell).

4) 3 continued... For Expansion Cohort 6 Only: Diagnosis of CLL that is naive to treatment and either: • Subject is age >/= 65 years; or • Subject has documented 17p- deletion or p53 mutation

5) For Dose Escalation/MTD Confirmation and Expansion Cohorts 1-5 Only: Progressed during, refractory to, intolerant of, or ineligible for established therapy, or has a disease for which there is no established therapy. There is no limit as to the maximum number of prior regimens.

6) An Eastern Cooperative Oncology Group (ECOG) performance status of 0 to 2.

7) Ability to adhere to the study visit schedule and all protocol requirements.

8) Voluntarily sign an informed consent form.

9) Patients must be able to receive outpatient treatment and laboratory monitoring (where specifically indicated) at the institution that administers study drug for the entire study.

10) Women of child-bearing potential (WCBP) (defined as a sexually mature woman who has not undergone surgical sterilization or who has not been naturally post-menopausal for at least 24 consecutive months for women </= 55 years or 12 consecutive months for women >55) must have a negative serum or urine beta human chorionic gonadotropin (betahCG) pregnancy test. All WCBP, all sexually active male patients, and all partners of patients should agree to use adequate methods of birth control throughout the study and for 30 days after the last dose of study drug.

11) Recovery to </= Grade 1 or baseline of any toxicities due to prior treatments, excluding alopecia.

Exclusion Criteria:1) Treatment with the following therapies within the specified time period: For Dose escalation/MTD confirmation Phase only: Any prior treatment with a PI3K inhibitor. • For Expansion Phase only: Prior PI3K inhibitor within 4 weeks of the start of IPI-145 administration • Tyrosine kinase inhibitor within 7 days of the start of IPI-145 administration. • Any chemotherapy with the exception of hydroxyurea and intrathecal (IT) prophylactic chemotherapy, radiation therapy (other than whole brain irradiation [WBI]), surgery or ablative therapy within 3 weeks of the start of IPI-145 administration. • Investigational therapy within 3 weeks of the start of IPI-145 administration. Investigational agents with a half-life of greater than 3 days, or with a half-life that is unknown, should be discussed with the medical monitor on a case-by-case basis. • Nitrosoureas or mitomycin C within 6 weeks of the start of IPI-145 administration.

2) Ongoing treatment with chronic immunosuppressants (e.g., cyclosporine following transplant or systemic steroids). For Expansion Phase Cohorts: systemic steroids are allowed at study treatment initiation with the intent to wean to physiologic replacement (< 10 mg prednisone QD) by end of treatment Cycle 1.

3) Patients with overt leptomeningeal leukemia or CNS lymphoma. Patients must be free of CNS disease for a minimum of 2 months. Patients with symptoms of CNS disease must have a negative diagnostic lumbar puncture prior to study enrollment.

4) Inadequate hepatic function defined by aspartate aminotransferase (AST) and/or alanine aminotransferase (ALT) >2.5 x upper limit of normal (ULN); direct bilirubin >1.5 x ULN.

5) For Dose escalation/MTD confirmation Phase Only: Inadequate bone marrow function defined by ANC < 750 cells/mm3, platelet count < 75,000 mm3, and a hemoglobin < 8 g/dL without transfusion or cytokine support for > 2 weeks prior to the start of study treatment. Patients who require transfusions or growth factor support are eligible.

6) Inadequate renal function defined by serum creatinine > 1.5 x ULN.

7) For Dose escalation/MTD confirmation Phase Only: Baseline QTcF > 450 ms. NOTE: This criterion does not apply to patients with a left bundle branch block. For Expansion Phase Cohorts: Baseline QTcF > 480 ms. NOTE: This criterion does not apply to patients with a left bundle branch block.

8) Concurrent treatment with any agent known to prolong the QTc interval.

9) Prior surgery affecting drug absorption or any gastrointestinal dysfunction that could alter drug absorption (e.g., gastric bypass surgery, gastrectomy).

10) Patients with a history of stroke, unstable angina, myocardial infarction, or ventricular arrhythmia requiring medication or mechanical control within the last 6 months.

11) Patients with a history of tuberculosis within the preceding two years.

12) Patients who have had a venous thromboembolic event (e.g., pulmonary embolism or deep vein thrombosis) requiring anticoagulation and who meet any of the following criteria: • Have been on a stable dose of anticoagulation for < 1 month • Have had a Grade 2, 3 or 4 hemorrhage in the last 30 days • Are experiencing continued symptoms from their venous thromboembolic event (e.g. continued dyspnea or oxygen requirement) NOTE: Patients who have had a venous thromboembolic event but do not meet any of the above three criteria are eligible for participation.

13) Patients with a history of alcohol abuse, chronic hepatitis, or other chronic liver disease (other than metastatic disease to the liver): NOTE: Chronic hepatitis includes active infection with hepatitis B or C. All patients will be tested for hepatitis C virus antibodies (HCV Ab) and hepatitis B surface antigen (HBsAg) at screening. Patients with a positive result for HBsAg or HCV Ab will be excluded from enrolling in this study.

14) Concurrent administration of medications or foods that are strong or moderate inhibitors or inducers of CYP3A.

15) Presence of active infection within 72 hours of treatment. Patients with ongoing use of prophylactic antibiotics are eligible as long as there is no evidence of active infection and the antibiotic is not included on the list of prohibited medications.

16) Significant co-morbid condition or disease which in the judgment of the Investigator would place the patient at undue risk or interfere with the study. Examples include, but are not limited to cirrhotic liver disease, sepsis, recent significant traumatic injury and other conditions.

17) Known human immunodeficiency virus (HIV) positivity.

18) Pregnant or lactating women.

19) Unable to receive prophylactic treatment for pneumocystis.

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Links
Registration Number: NCT01476657
Study Information on Clinical Trials Registry (clinicaltrials.gov)

Other Links:
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Results


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