Return to List

Study Summary
No. 2012-0171:.......Leukemia......Susan O'Brien......Leukemia
.
Study Summary Title
Study Summary
Number:
2012-0171
Study Title:A Phase 3, Randomized, Double-Blind, Placebo-Controlled Study Evaluating the Efficacy and
Safety of GS-1101 (CAL-101) in Combination with Rituximab for Previously Treated Chronic Lymphocytic
Leukemia
.
Physician New Patient Referral
Name:Susan O'BrienPatients Call:800-392-1611 (in U.S.A.) 713-792-6161 (outside U.S.A.)
Dept:LeukemiaReferring MD
Call:
800-392-1611 (in U.S.A.) 713-792-6161 (outside U.S.A.)
Phone:713-792-7543
Contact us about clinical trials
.
General Information
Disease Group:LeukemiaSupported By:Gilead Sciences
Phase of Study:Phase IIIReturn
Visit:
Treatment
Agents:
GS-1101Home Care:
Treatment Loc:Both at MDACC & and Other Sites
Estimated
Length of Stay
in Houston:
Description/
Intervention:
The goal of this clinical research study is to find out if adding GS-1101 to
treatment with rituximab is more effective in controlling CLL than treatment
with rituximab alone. The safety of this drug combination will also be
studied.

Rituximab is designed to attach to cancer cells and damage them, which may
cause the cells to die.

GS-1101 is designed to block some of the cell functions that cause CLL cells to
grow and survive.

A placebo is not a drug. It looks like the study drug but is not designed to
treat any disease or illness. It is designed to be compared with a study drug
to learn if the study drug has any real effect.
.
Study Objectives / Outcomes
Primary Objective:
Evaluate the effect of the addition of GS-1101 to rituximab on PFS.

Secondary Objective:
Determine the effect of the addition of GS-1101 to rituximab on the onset, magnitude, and duration of tumor control; overall survival (OS); health-related quality of life (HRQL); changes in subject performance status; disease-associated biomarkers and potential mechanisms of resistance; treatment administration; safety; and health resource utilization.
.
Study Status Information
Study Activation / Registration Date:
IRB Review and Approval Date:10/18/2012
Study Type:Phase Iii
Recruitment Status:Open
Projected Accrual:~160
.
Enrollment Eligibility
If you do not meet the enrollment eligibility, there may be other treatment options for you. Please Contact the Referral Office for more information.

Inclusion Criteria:1) Male or female >/= 18 years of age.

2) Diagnosis of B-cell CLL, with diagnosis established according to IWCLL criteria and documented within medical records.

3) CLL that warrants treatment (consistent with accepted criteria for initiation of therapy). Any of the following conditions constitute CLL that warrants treatment: a) Evidence of progressive marrow failure as manifested by the onset or worsening of anemia and/or thrombocytopenia, b) Massive (ie, lower edge of spleen >/= 6 cm below the left costal margin), progressive, or symptomatic splenomegaly, or c) Massive (ie, >/= 10 cm in the longest diameter), progressive, or symptomatic lymphadenopathy, or d) Progressive lymphocytosis in the absence of infection, with an increase in blood ALC>/= 50% over a 2-month period or lymphocyte doubling time of <6 months (as long as initial ALC was ≥30,000/L), or

4) (Continued) e) Autoimmune anemia and/or thrombocytopenia that is poorly responsive to corticosteroids or other standard therapy, or f) Constitutional symptoms, defined as any one or more of the following disease-related symptoms or signs occurring in the absence of evidence of infection: i) Unintentional weight loss of >/= 10% within the previous 6 months, or ii) Significant fatigue (>/= Grade 2), or iii) Fevers >100.5°F or 38.0°C for >/= 2 weeks, or iv) Night sweats for >1 month.

5) Presence of radiographically measurable lymphadenopathy (defined as the presence of >/= 1 nodal lesion that measures >/= 2.0 cm in the longest dimension [LD] and >/= 1.0 cm in the longest perpendicular dimension [LPD] as assessed by CT or MRI).

6) Prior treatment for CLL comprising any of the following: a) Prior treatment with >/=1 regimen containing a therapeutic anti-CD20 antibody (eg, rituximab, ofatumumab, GA-101) administered for >/=2 doses of antibody treatment, or b) Prior treatment with >/=2 regimens containing >/=1 cytotoxic agent (eg, fludarabine, pentostatin, cladribine, cyclophosphamide, chlorambucil, bendamustine) administered for >/=2 cycles of cytotoxic treatment Note: Prior anti-CD20 antibody or cytotoxic drugs may have been administered as single agents or as components of combination therapies. Subjects may also have received other commercially available therapies (eg, alemtuzumab, lenalidomide, corticosteroids, or others) or non-excluded investigational therapies. Each repeated course of the same single-agent or combination is considered an independent regimen.

7) In a subject whose last prior therapy contained an anti-CD20 antibody (eg, rituximab, ofatumumab, GA-101), evidence of disease improvement during that therapy or documentation of CLL progression >/=6 months after completion of that therapy. Note: Subjects who did not receive a therapeutic anti-CD20 antibody (eg, rituximab, ofatumumab, GA-101) as a component of the last prior therapy need not have experienced disease improvement or may have relapsed <6 months from the completion of the prior regimen.

8) Documentation of CLL progression <24 months since the completion of the last prior therapy for CLL.

9) Discontinuation of all therapy (including radiotherapy, chemotherapy, immunotherapy, systemic corticosteroids, or investigational therapy) for the treatment of CLL >/=3 weeks before randomization.

10) All acute toxic effects of any prior antitumor therapy resolved to Grade </=1 before randomization (with the exception of alopecia [Grade 1 or 2 permitted], neurotoxicity [Grade 1 or 2 permitted], or bone marrow parameters [Grades 1, 2, 3, or 4 permitted).

11) Karnofsky performance score of >/=40.

12) Appropriate for non-cytotoxic-containing therapy based on the presence of any of the following factors: a) Grade >/=3 neutropenia or thrombocytopenia attributable to cumulative myelotoxicity from prior administration of cytotoxic agents (as documented by bone marrow biopsy obtained since last prior therapy), or b) Estimated creatinine clearance (eCCr) <60 mL/min (as determined by the Cockcroft-Gault method), or c) A CIRS score of >6.

13) Required baseline laboratory data (within 4 weeks prior to randomization) as shown in the table below. Note: Confirmation should be considered for out-of-range values to determine if the abnormality is real or artifactual. Values should be obtained within the screening period and should generally be the most recent measurement obtained. Subjects with any degree of neutropenia, thrombocytopenia, or anemia due to CLL or prior therapy may enroll.

14) For female subjects of childbearing potential, willingness to abstain from heterosexual intercourse or use a protocol-recommended method of contraception from the screening visit (Visit 1) throughout the study treatment period and for 30 days following the last dose of study drug. Note: A female subject is considered to be of childbearing potential unless she has had a hysterectomy, bilateral tubal ligation, or bilateral oophorectomy, has medically documented ovarian failure (with serum estradiol and folliclestimulating hormone [FSH] levels within the institutional postmenopausal range and a negative serum or urine βHCG), or is menopausal (age ≥55 years with amenorrhea for ≥6 months).

15) For male subjects of childbearing potential and having intercourse with females of childbearing potential, willingness to abstain from heterosexual intercourse or use a protocol-recommended method contraception from the randomization visit (Visit 2) throughout the study treatment period and for 90 days following the last dose of study drug and to refrain from sperm donation from randomization (Visit 2) throughout the study treatment period and for 90 days following the last dose of study drug. Note: A male subject is considered able to father a child unless he has had a bilateral vasectomy with documented aspermia or a bilateral orchiectomy, or has ongoing testicular suppression with a depot luteinizing hormone-releasing hormone (LH-RH) agonist (eg, goserelin acetate [Zoladex®]), leuprolide acetate [Lupron®]), or triptorelin pamoate [Trelstar®]).

16) In the judgment of the investigator, participation in the protocol offers an acceptable benefit-to-risk ratio when considering current CLL disease status, medical condition, and the potential benefits and risks of alternative treatments for CLL.

17) Willingness to comply with scheduled visits, drug administration plan, imaging studies, laboratory tests, other study procedures, and study restrictions. Note: Psychological, social, familial, or geographical factors that might preclude adequate study participation should be considered.

18) Evidence of a personally signed informed consent indicating that the subject is aware of the neoplastic nature of the disease and has been informed of the procedures to be followed, the experimental nature of the therapy, alternatives, potential benefits, possible side effects, potential risks and discomforts, and other pertinent aspects of study participation.

Exclusion Criteria:1) Known histological transformation from CLL to an aggressive lymphoma (ie, Richter transformation). Note: Biopsy documentation of the absence or presence of transformation is not required.

2) Presence of intermediate- or high-grade myelodysplastic syndrome (ie, subjects are excluded who have>/=5 bone marrow blasts; karotypic abnormalities other than normal, Y deletion, 5q deletion, or 20q deletion; or >/=2 lineages of cytopenias)

3) History of a non-CLL malignancy except for the following: adequately treated local basal cell or squamous cell carcinoma of the skin, cervical carcinoma in situ, superficial bladder cancer, asymptomatic prostate cancer without known metastatic disease and with no requirement for therapy or requiring only hormonal therapy and with normal prostate-specific antigen for >/=1 year prior to randomization, other adequately treated Stage 1 or 2 cancer currently in complete remission, or any other cancer that has been in complete remission for >/=5 years.

4) Evidence of ongoing systemic bacterial, fungal, or viral infection at the time of initiation of randomization (Visit 2). Note: Subjects with localized fungal infections of skin or nails are eligible. Subjects may be receiving prophylactic antiviral or antibacterial therapies at the discretion of the investigator; anti-pneumocystis prophylaxis is encouraged. For subjects who are at substantial risk of an infection (eg, influenza) that may be prevented by immunization, consideration should be given to providing the vaccine prior to initiation of protocol therapy.

5) Known history of drug-induced liver injury, chronic active hepatitis C (HCV), chronic active hepatitis B (HBV), alcoholic liver disease, non-alcoholic steatohepatitis, primary biliary cirrhosis, ongoing extrahepatic obstruction caused by cholelithiasis, cirrhosis of the liver, or portal hypertension.

6) Known history of drug-induced pneumonitis.

7) Ongoing inflammatory bowel disease.

8) Ongoing alcohol or drug addiction.

9) Pregnancy or breastfeeding.

10) History of prior allogeneic bone marrow progenitor cell or solid organ transplantation.

11) Ongoing immunosuppressive therapy, including systemic corticosteroids for treatment of CLL. Note: Subjects may use topical, enteric, or inhaled corticosteroids as therapy for comorbid conditions and systemic steroids for autoimmune anemia and/or thrombocytopenia. Ongoing use of low-dose systemic corticosteroids (</=5 mg/day of methylprednisolone or equivalent) for rheumatologic conditions is permitted. During study participation, subjects may receive systemic or other corticosteroids as pretreatment for rituximab infusions or as needed for treatment-emergent comorbid conditions.

12) Prior therapy with any inhibitor of Bruton tyrosine kinase (BTK), Janus kinase (JAK), mammalian target of rapamycin (mTOR), phosphatidylinositol 3 kinase (PI3K) (including GS 1101), or spleen tyrosine kinase (Syk).

13) History of anaphylaxis in association with previous administration of monoclonal antibodies

14) Concurrent participation in another therapeutic clinical trial.

15) Prior or ongoing clinically significant illness, medical condition, surgical history, physical finding, electrocardiogram (ECG) finding, or laboratory abnormality that, in the investigator's opinion, could adversely affect the safety of the subject or impair the assessment of study results.

.
Links
Registration Number: NCT01539512
Study Information on Clinical Trials Registry (clinicaltrials.gov)

Other Links:
.
Results


Return to Clinical Trials at M.D. Anderson Cancer Center