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Study Summary
No. 2012-0411:.......Leukemia......Susan O'Brien......Leukemia
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Study Summary Title
Study Summary
Number:
2012-0411
Study Title:A Phase 3, Randomized, Double-Blind, Placebo-Controlled Study Evaluating the Efficacy and Safety of GS-1101 (CAL-101) in Combination with Bendamustine and Rituximab for Previously Treated Chronic Lymphocytic Leukemia
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Physician New Patient Referral
Name:Susan O'BrienPatients Call:800-392-1611 (in U.S.A.) 713-792-6161 (outside U.S.A.)
Dept:LeukemiaReferring MD
Call:
800-392-1611 (in U.S.A.) 713-792-6161 (outside U.S.A.)
Phone:713-792-7543
Contact us about clinical trials
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General Information
Disease Group:LeukemiaSupported By:Gilead Sciences, Inc.
Phase of Study:Phase IIIReturn
Visit:
Treatment
Agents:
Bendamustine HCl
GS-1101
Rituximab
Home Care:
Treatment Loc:Both at MDACC & and Other Sites
Estimated
Length of Stay
in Houston:
Description/
Intervention:
The goal of this clinical research study is to find out if adding GS-1101 to
standard treatment with rituximab and bendamustine is more effective than
standard treatment plus a placebo, in controlling CLL. The safety of these 2
treatment combinations will also be studied.

GS-1101 is designed to block one of the signals inside the cells that may cause
cancer to grow and survive. By blocking this signal, GS-1101 may reduce the
cancer or prevent it from growing and surviving.

Bendamustine is designed to damage and destroy the DNA (genetic material) of
cancer cells.

Rituximab is designed to attach to cancer cells and damage them, which may
cause the cells to die.

A placebo is not a drug. It looks like the study drug but is not designed to
treat any disease or illness. It is designed to be compared with a study drug
to learn if the study drug has any real effect.
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Study Objectives / Outcomes
Primary Objective:
  • To evaluate the effect of the addition of GS-1101 to bendamustine/rituximab on PFS in subjects with previously treated CLL

Secondary Objectives:
  • To determine the effect of the addition of GS-1101 to bendamustine/rituximab on the onset, magnitude, and duration of tumor control
  • To assess the effect of the addition of GS-1101 to bendamustine/rituximab on measures of subject well-being, including OS, HRQL, and performance status
  • To assess the effects of the addition of GS-1101 to bendamustine/rituximab on disease associated biomarkers and to evaluate potential mechanisms of resistance to GS-1101
  • To characterize exposure to study treatment as determined by treatment administration with each of the therapeutic agents and evaluation of GS-1101 plasma concentrations over time
  • To describe the safety profile observed with the addition of GS-1101 to bendamustine/rituximab
  • To estimate health resource utilization associated with the addition of GS-1101 to bendamustine/rituximab
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Study Status Information
Study Activation / Registration Date:
IRB Review and Approval Date:12/07/2012
Study Type:Phase Iii
Recruitment Status:Open
Projected Accrual:390 (~195 subjects per treatment arm)
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Enrollment Eligibility
If you do not meet the enrollment eligibility, there may be other treatment options for you. Please Contact the Referral Office for more information.

Inclusion Criteria:1) Male or female >/= 18 years of age

2) Diagnosis of B-cell CLL, with diagnosis established according to International Workshop on Chronic Lymphocytic Leukemia (IWCLL) criteria and documented within medical records

3) CLL that warrants treatment (consistent with accepted IWCLL criteria for initiation of therapy). Any of the following conditions constitute CLL that warrants treatment: a) Evidence of progressive marrow failure as manifested by the onset or worsening of anemia and/or thrombocytopenia b) Massive (ie, lower edge of spleen >/=6 cm below the left costal margin), progressive, or symptomatic splenomegaly, or c) Massive (ie, >/=10 cm in the longest diameter), progressive, or symptomatic lymphadenopathy, or d) Progressive lymphocytosis in the absence of infection, with an increase in blood absolute lymphocyte count (ALC) >/=50% over a 2-month period or lymphocyte doubling time of <6 months (as long as initial ALC was >/=30,000/L), or e) Autoimmune anemia and/or thrombocytopenia that is poorly responsive to corticosteroids or other standard therapy, or

4) (Continued) f) Constitutional symptoms, defined as any one or more of the following disease-related symptoms or signs occurring in the absence of evidence of infection: i) Unintentional weight loss of >/=10% within the previous 6 months, or ii) Significant fatigue (>/=Grade 2), or iii) Fevers >100.5°F or 38.0°C for >/=2 weeks, or iv) Night sweats for >1 month.

5) Presence of measurable lymphadenopathy (defined as the presence of >/=1 nodal lesion that measures >/=2.0 cm in the longest dimension and >/=1.0 cm in the longest perpendicular dimension as assessed by computed tomography or magnetic resonance imaging

6) Prior treatment for CLL comprising: a) >/=2 cycles of a regimen containing a purine analog (eg, fludarabine, pentostatin, cladribine) or bendamustine, and b) >/=2 doses with a regimen containing an anti-CD20 monoclonal antibody (eg, rituximab, ofatumumab, GA-101). Note: Prior cytotoxic drugs or anti-CD20 antibodies may have been administered as single agents or as components of combination therapies. Subjects may also have received other commercially available therapies (eg, alemtuzumab, lenalidomide, corticosteroids, or others) or non-excluded investigational therapies. Each repeated but separated therapeutic application of the same single-agent or combination is considered an independent regimen.

7) Documentation of CLL progression <36 months since the completion of the last prior therapy for CLL.

8) Discontinuation of all therapy (including radiotherapy, chemotherapy, immunotherapy, systemic corticosteroids, or investigational therapy) for the treatment of CLL >/=3 weeks before randomization.

9) All acute toxic effects of any prior antitumor therapy resolved to Grade </=1 before randomization (with the exception of alopecia (Grade 1 or 2 permitted), neurotoxicity (Grade 1 or 2 permitted), or bone marrow parameters (Grades 1 or 2 permitted).

10) Karnofsky performance score of >/=60.

11) Required baseline laboratory data (within 4 weeks prior to randomization). Note: Confirmation should be considered for out-of range values to determine if the abnormality is real or artifactual. Values should be obtained within the screening period and should generally be the most recent measurement obtained. CLL peripheral blood or bone marrow evaluations within 12 weeks (FISH, DNA mutational analysis, flow cytometry, and cytology).

12) For female subjects of childbearing potential, willingness to abstain from heterosexual intercourse or use a protocol-recommended method of contraception from the screening visit (Visit 1) throughout the study treatment period and for 30 days following the last doe of study drug. Note: A female subject is considered to be of childbearing potential unless she has had a hysterectomy, bilateral tubal ligation, or bilateral oophorectomy; has medically documented ovarian failure (with serum estradiol and follicle-stimulating hormone (FSH) levels within the institutional postmenopausal range and a negative serum or urine BHCG); or is menopausal (age greater than or equal to 55 years with amenorrhea for greater than or equal to 6 months).

13) For male subjects of childbearing potential having intercourse with females of childbearing potential, willingness to abstain from heterosexual intercourse or use a protocol-recommended method of contraception from the randomization visit (Visit 2) throughout the study treatment period and for 90 days following the last dose of study drug and to refrain from sperm donation from randomization (Visit 2) throughout the study treatment period and for 90 days following the last dose of study drug. Note: A male subject is considered able to father a child unless he has had a bilateral vasectomy with documented aspermia or a bilateral orchiectomy, or has ongoing testicular suppression with a depot luteinizing hormone-releasing hormone (LH-RH) agonist (eg, goserelin acetate (Zoladex), leuprolide acetate (Lupron), or triptorelin pamoate (Trelstar).

14) In the judgment of the investigator, participation in the protocol offers an acceptable benefit-to-risk ratio when considering current CLL disease status, prior treatment history, medical condition, and the potential benefits and risks of alternative treatments for CLL. Note: Investigators should consider whether a study subject is an appropriate candidate for bendamustine-containing therapy based on the number and severity of comorbid conditions; subjects with a baseline Cumulative Illness Rating Scale (CIRS) score of </=6 may be particularly appropriate candidates for this trial.

15) Willingness and ability to comply with scheduled visits, drug administration plan, imaging studies, laboratory tests, other study procedures, and study restrictions. Note: Psychological, social, familial, or geographical factors that might preclude adequate study participation should be considered.

16) Evidence of a personally signed informed consent indicating that the subject is aware of the neoplastic nature of the disease and has been informed of the procedures to be followed, the experimental nature of the therapy, alternatives, potential benefits, possible side effects, potential risks and discomforts, and other pertinent aspects of study participation.

Exclusion Criteria:1) Known histological transformation from CLL to an aggressive lymphoma (ie, Richter transformation). Note: Biopsy documentation of the absence or presence of transformation is not required.

2) Known presence of intermediate- or high-grade myelodysplastic syndrome (ie, subjects are excluded who have >/=5 bone marrow blasts; karotypic abnormalities other than normal, Y deletion, 5q deletion, or 20q deletion; or >/=2 lineages of cytopenias due to myelodysplasia).

3) History of a non-CLL malignancy except for the following: adequately treated local basal cell or squamous cell carcinoma of the skin, cervical carcinoma in situ, superficial bladder cancer, asymptomatic prostate cancer without known metastatic disease and with no requirement for therapy or requiring only hormonal therapy and with normal prostate-specific antigen for >/=1 year prior to randomization, other adequately treated Stage 1 or 2 cancer currently in complete remission, or any other cancer that has been in complete remission for >/=5 years.

4) Evidence of ongoing systemic bacterial, fungal, or viral infection at the time of randomization (Visit 2). Note: Subjects with localized fungal infections of skin or nails are eligible. Subjects may be receiving prophylactic antiviral or antibacterial therapies at the discretion of the investigator. For subjects who are at substantial risk of an infection (eg, influenza) that may be prevented by immunization, consideration should be given to providing the vaccine prior to initiation of protocol therapy.

5) Ongoing drug-induced liver injury, chronic active hepatitis C (HCV), chronic active hepatitis B (HBV), alcoholic liver disease, non-alcoholic steatohepatitis, primary biliary cirrhosis, ongoing extrahepatic obstruction caused by cholelithiasis, cirrhosis of the liver, or portal hypertension.

6) Ongoing drug-induced pneumonitis.

7) Ongoing inflammatory bowel disease.

8) Ongoing alcohol or drug addiction.

9) Pregnancy or breastfeeding.

10) History of prior allogeneic bone marrow progenitor cell or solid organ transplantation.

11) Ongoing immunosuppressive therapy, including systemic corticosteroids for treatment of CLL. Note: Subjects may use topical, enteric, or inhaled corticosteroids as therapy for comorbid conditions and systemic steroids for autoimmune anemia and/or thrombocytopenia. Ongoing use of low-dose systemic corticosteroids (</=5 mg/day of methylprednisolone or equivalent) for rheumatologic conditions is permitted. During study participation, subjects may receive systemic or other corticosteroids as pretreatment for rituximab infusions or as needed for treatment-emergent comorbid conditions.

12) In a subject with a history of prior bendamustine therapy, a time interval from the last dose of bendamustine to the subsequent CLL progression of <6 months.

13) History of prior therapy with any inhibitor of AKT, Bruton tyrosine kinase (BTK), Janus kinase (JAK), mammalian target of rapamycin (mTOR), phosphatidylinositol 3-kinase (PI3K) (including GS-1101), or spleen tyrosine kinase (SYK).

14) History of anaphylaxis in association with previous administration of monoclonal antibodies

15) Concurrent participation in another therapeutic clinical trial.

16) Prior or ongoing clinically significant illness, medical condition, surgical history, physical finding, electrocardiogram (ECG) finding, or laboratory abnormality that, in the investigator's opinion, could adversely affect the safety of the subject or impair the assessment of study results.

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Links
Registration Number: NCT01569295
Study Information on Clinical Trials Registry (clinicaltrials.gov)

Other Links:
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Results


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