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Study Summary
No. COGARET0332:.......Eye; Pediatrics; Solid Tumors......Cynthia E. Herzog......Pediatrics
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Study Summary Title
Study Summary
Number:
COGARET0332
Study Title:A Study of Unilateral Retinoblastoma With and Without Histopathologic High-Risk Features and the Role of Adjuvant Chemotherapy
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Physician New Patient Referral
Name:Cynthia E. HerzogPatients Call:800-392-1611 (in U.S.A.) 713-792-6161 (outside U.S.A.)
Dept:PediatricsReferring MD
Call:
800-392-1611 (in U.S.A.) 713-792-6161 (outside U.S.A.)
Phone:713-792-6620
Contact us about clinical trials
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General Information
Disease Group:Eye
Pediatrics
Solid Tumors
Supported By:NCI through COG
Phase of Study:Phase IIIReturn
Visit:
Patients with high risk features must return for chemotherapy cycles and
physical exams every 28 days
Patients with low risk features will return for follow up exams every 3 months
for first year, 6 months for second year and then annually
Treatment
Agents:
Carboplatin
Etoposide
Vincristine
Home Care:Supportive care only: routine antibiotics and topical steroids as determined by
the local physician
Treatment Loc:Both at MDACC & outside MDACC at one or more Collaborating Sites or Institutions
Estimated
Length of Stay
in Houston:
Patients with high risk features will require inpatient hospitalization for at
least two days during chemotherapy treatments out of every 28 days, and may
require inpatient hospitalization intermittently between cycles of chemotherapy
Description/
Intervention:
The goal of this clinical research study is to collect information about
patients who have retinoblastoma in only one eye and have had the eye removed.
The study doctors want to find out if the chemotherapy can keep the cancer from
coming back in patients who are considered at "high-risk" for the disease to
come back or spread to other parts of the body.
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Study Objectives / Outcomes
To prospectively determine the prevalence of high-risk histopathologic features such as choroidal
involvement, optic nerve invasion, scleral and anterior segment involvement in patients with unilateral
retinoblastomas who had undergone enucleation

To demonstrate that patients without certain high-risk features can be successfully treated with
enucleation alone by estimating the event-free survival (EFS) and overall survival (S) where an event is
defined as the occurrence of extraocular or metastatic disease.

To estimate the event-free survival (EFS) and overall survival (S) in patients with specific high-risk
features who are uniformly treated with adjuvant chemotherapy where an event is defined as the
occurrence of extraocular or metastatic disease.

To estimate the incidence of toxicities associated with the proposed adjuvant chemotherapy.
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Study Status Information
Study Activation / Registration Date:11/21/2006
IRB Review and Approval Date:07/05/2006
Study Type:Phase Iii
Recruitment Status:Closed
Projected Accrual:300
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Enrollment Eligibility
If you do not meet the enrollment eligibility, there may be other treatment options for you. Please Contact the Referral Office for more information.

Inclusion Criteria:1) Only patients who are between and including the ages of 0 to 6 years at study entry are eligible.

2) All diagnosed children with Retinoblastoma with unilateral disease who undergo enucleation as initial therapy. Patients with or without high-risk histopathologic features will be eligible. High-risk features are defined as: a) Posterior uveal invasion (includes choroidal invasion) b) Any degree of concomitant choroid and optic nerve involvement. c) Tumor involving the optic nerve posterior to the lamina cribrosa as an independent finding. d) Scleral invasion e) Anterior chamber seeding. f) Ciliary body infiltration g) Iris infiltration

3) Evidence of choroidal and/or optic nerve invasion past the lamina cribosa ARE ALLOWED. Since pathology may not be available at study entry on an enucleated eye, patients may be entered on study pending final pathology report. (If histology meets exclusion criteria, then patient will be off study.)

4) The individual institution must submit slides for central review as per guidelines and within 21 calendar days after surgery. (If the slides are not shipped within 21 calendar days of surgery, the patient will be ineligible for the study.)

5) Lansky score greater than or equal to 50

6) No prior therapy other than enucleation

7) CT/MRI of the brain: Baseline CT/MRI of the brain to be performed either prior to enucleation or within 5 weeks of enucleation. Patients who will receive chemotherapy should have a baseline CT/MRI performed prior to initiation of chemotherapy.

8) CBC is required prior to enrollment in all patients.

9) Patients with High-Risk features only: Hematologic function defined as: Hemoglobin gm/dl > 8; and ANC >/= 1000/µL; and platelet count >/= 100,000/µL.

10) Patients with High-Risk features only: 1) Creatinine clearance or radioisotope GFR >/= 70 ml/min/1.73 m^2; OR, 2) maximum serum creatinine (md/dL) based on age/gender as follows: 1 month to < 6 months: 0.4 md/dL; 6 months to < 1 yr: 0.5 md/dL; 1 to < 2 yrs: 0.6 md/dL; 2 to < 6 yrs: 0.8 md/dL; 6 to < 10 yrs: 1 md/dL; 10 to < 13 yrs: 1.2 md/dL; 13 to < 16 yrs: Male: 1.5 md/dL; Female: 1.4 md/dL; >/= 16 yrs: Male: 1.7 md/dL; Female: 1.4 mg/dL.

11) Patients with High-Risk features only: Adequate liver function defined as:Total bilirubin </= 1.5 x upper limit of normal (ULN) for age, and SGOT (AST) or SGPT (ALT) < 2.5 x upper limit of normal (ULN) for age.

12) Study enrollment AND pathology slide submission MUST take place within 21 calendar days of enucleation. Patients must be enrolled BEFORE adjuvant chemotherapy begins. The date adjuvant chemotherapy is to start, if chemotherapy is indicated as per protocol, must be no later than 35 calendar days after the date of enucleation. All patients must sign the initial consent form after enucleation, but prior to study enrollment and prior to submission of slides for review.

13) All patients and/or their parents or legal guardians must sign a written informed consent.

14) Subjects, for whom adjuvant chemotherapy is recommended, must also sign the second consent form (chemotherapy arm) prior to initiation of chemotherapy. (Treatment must start within 35 days of enucleation.)

Exclusion Criteria:1) Patients > 6 years of age

2) Patients who received chemotherapy prior to Study Entry.

3) Patients who had previously received laser and/or cryotherapy.

4) Patients with any evidence of extraocular retinoblastoma clinically or by CT/MRI of brain and orbits with and without gadolinium (preferred study)

5) Patients with tumor present on histologic examination at the cut end of the optic nerve on any eye enucleated prior to study entry.

6) Patients with evidence of systemic metastases on bone marrow, bone scan, and/or any other additional tests done at study entry are NOT eligible (Note: these tests are required only with specific indications: Bone marrows are also required if CBC is abnormal at study entry. Bone scan only required if patient has symptomatic bone pain to rule out systemic metastases.)

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Links
Registration Number: NCT00335738
Study Information on Clinical Trials Registry (clinicaltrials.gov)

Other Links:
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Results


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