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Study Summary
No. 2007-0869:.......Bone; Pediatrics......Peter M. Anderson......Pediatrics
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Study Summary Title
Study Summary
Number:
2007-0869
Study Title:Liposomal Muramyl Tripeptide Phosphatidyl Ethanolamine (L-MTP-PE): Compassionate Access for High-risk Osteosarcoma
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Physician New Patient Referral
Name:Peter M. AndersonPatients Call:800-392-1611 (in U.S.A.) 713-792-6161 (outside U.S.A.)
Dept:PediatricsReferring MD
Call:
800-392-1611 (in U.S.A.) 713-792-6161 (outside U.S.A.)
Phone:713-792-6620
Contact us about clinical trials
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General Information
Disease Group:Bone
Pediatrics
Supported By:Millennium: the Takeda Oncology Company.
Phase of Study:N/AReturn
Visit:
Maximum: 36 weeks total: Twice weekly for 12 weeks, then once weekly for 24
additional weeks.
Patients may recieve some treatment at a participating center other than MDACC.
Treatment
Agents:
Liposomal MTP-PEHome Care:Supportive medications may be given at home.
Treatment Loc:Both at MDACC & outside MDACC at one or more Collaborating Sites or Institutions
Estimated
Length of Stay
in Houston:
Hospitalization is not anticipated for L-MTP-PE; it is an outpatient 1 hour
infusion. The protocol stipulates that L-MTP-PEshould be used with outpatient
chemotherapy regimens. However, patients in the hospital for other reasons may
get L-MTP-PE.
Description/
Intervention:
The goal of the compassionate access study is to provide an investigational
drug, liposomal muramyl tripeptide phosphatidyl ethanolamine (L-MTP-PE) alone
or combined with recommended approved therapy to you for treatment of
osteosarcoma. Compassionate access is a way to make a drug that showed an
improvement in survival responses available while it is still being tested.
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Study Objectives / Outcomes
Primary Objective
To collect information regarding the safety and tolerability of L-MTP-PE

Secondary Objectives
· To assess outcomes of patients who receive L-MTP-PE
· To evaluate serum concentration-time profiles of free and total L-MTP-PE in
15-20 patients
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Study Status Information
Study Activation / Registration Date:
IRB Review and Approval Date:01/24/2008
Study Type:Other
Recruitment Status:Terminated
Projected Accrual:200
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Enrollment Eligibility
If you do not meet the enrollment eligibility, there may be other treatment options for you. Please Contact the Referral Office for more information.

Inclusion Criteria:1) Signed informed consent/assent by the patient or his/her legal guardian. Voluntary participation in the pharmacokinetic portion of the compassionate access protocol will be included in the informed consent but not required for compassionate use participation.

2) Documented diagnosis of high grade osteosarcoma in patients with relapsed or recurrent disease, locally or metastatic, resectable or unresectable, who have failed prior recommended chemotherapy or have received an abbreviated chemotherapy regimen secondary to toxicity (e.g. hypophosphatemia from ifosfamide, cardiotoxicity from doxorubicin, renal dysfunction from methotrexate, ifosfamide, or cisplatin).

3) Ages 2 < / = 50 years.

4) Adequate hematopoietic function as demonstrated by: 1) Absolute Neutrophil Count (ANC) > 750/microL; Hemoglobin (Hb) > 8 g/dL; Platelets > 30,000/microL.

5) Adequate hepatic function as documented by 1) ALT < 2.5 x upper limit of normal (ULN) for age; 2) total bilirubin < / = 1.5 x ULN for age.

6) Adequate renal function as demonstrated by: 1) Creatinine clearance or radioisotope glomerular filtration rate > 70 mL/min/1.73 m^2; OR, 2) Serum creatinine < / = 2x ULN for age.

7) Absence of concurrent active acute infection (i.e., afebrile).

8) In females of child bearing potential (not menopausal for 12 months or no previous surgical sterilization), negative pregnancy test. All sexually active subjects will use an effective means of contraception. Such means include oral contraceptives, Lupron Depot, DepoProvera, and condom with diaphragm and spermicidal jelly).

9) Performance status: Lansky 50-100% (< / = 16 years of age); OR, ECOG 0-2 or Karnofsky 50-100% (>16 years of age).

Exclusion Criteria:1) Chronic use of corticosteroids or other immunosuppressive agents.

2) Patients who are pregnant or breast-feeding.

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Links
Registration Number: NCT00631631
Study Information on Clinical Trials Registry (clinicaltrials.gov)

Other Links:
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Results


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